PRKN (O60260) variants and mutations

PRKN (also known as O60260) is a human protein-coding gene encoding an e3 ubiquitin-protein ligase parkin protein. Its parkin ubiquitin-ligase activity marks damaged mitochondrial proteins after PINK1 activation and helps eliminate dysfunctional mitochondria through mitophagy. Biallelic loss-of-function variants are a major cause of autosomal recessive juvenile or early-onset Parkinson disease. This analysis covers 1,032 PRKN variants and mutations. Of these, 88% have computational variant effect predictions. Disease context includes Young adult-onset Parkinsonism, young-onset Parkinson disease, and lung cancer. Example PRKN variants include M1?, M1T, and I2M.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.

Notable PRKN variants

Examples include M1?, M1T, I2M, I2T, I2V, V3L, R6G, R6S. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.