PKD1 (Polycystin-1) variants and mutations
PKD1 (also known as Polycystin-1) is a human protein-coding gene encoding a polycystin-1 protein. Together with polycystin-2, it participates in tubular signaling, mechanosensation, and maintenance of renal epithelial architecture. Loss-of-function variants are the most common cause of autosomal dominant polycystic kidney disease. This analysis covers 7,773 PKD1 variants and mutations. Of these, 86% have computational variant effect predictions. Disease context includes autosomal dominant polycystic kidney disease, cystic kidney disease, and hypertensive disorder. Example PKD1 variants include M1I, P2S, and P3R.
Variant analysis overview
- Gene: PKD1
- Protein: Polycystin-1
- UniProt accession: P98161
- Organism: Homo sapiens
- Variants analyzed: 7773
- Variant scope: all variants
- Completed: 2026-08-18
Variant and mutation evidence
- Variant composition: 7,435 unspecified-consequence records; 3 stop lost; 151 synonymous variants; 156 missense variants; 5 in-frame deletions; 13 frameshift variants; 2 in-frame insertions; 1 stop-gained variants; 2 splice-region variants; 4 substitution
- Prediction scores: 6,677 variants have prediction scores (86% of the analyzed set).
Clinical, disease, and population context
- Disease context: 25 disease associations are represented. Top associations: autosomal dominant polycystic kidney disease, cystic kidney disease, hypertensive disorder, polycystic kidney disease, stage 5 chronic kidney disease, Renal insufficiency, autosomal recessive polycystic kidney disease, chronic kidney disease, kidney failure, Genetic renal or urinary tract malformation, hypertensive nephropathy, urinary system disorder.
Protein structure and variant hotspots
- Protein features: 11 transmembrane segments; 25 domains; 61 post-translational modification sites.
- Structural context: 5,215 variants have structural context.
- PTM context: 111 variants overlap post-translational modification sites.
Data sources
Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.
Notable PKD1 variants
Examples include M1I, P2S, P3R, P3T, A4P, P6L, P6S, A7T. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.
- M1I (p.Met1Ile), rs1567233098, ClinGen CA394283358, ClinVar RCV000712618, Pathogenic
- P2S (p.Pro2Ser), cosmic curated COSV10877, TOPMed rs2092942106, gnomAD rs2092942106, REVEL 0.03, MetaLR 0.04
- P3R (p.Pro3Arg), 1000Genomes rs937825645, TOPMed rs937825645, gnomAD rs937825645, REVEL 0.04, MetaLR 0.04, Uncertain significance, Polycystic kidney disease, adult type
- P3T (p.Pro3Thr), TOPMed rs1457976484, REVEL 0.06, MetaLR 0.05
- A4P (p.Ala4Pro), rs2544960800, ClinGen CA394283314, ClinVar RCV002470556, REVEL 0.05, MetaLR 0.04, Uncertain significance, Polycystic kidney disease, adult type
- P6L (p.Pro6Leu), Ensembl rs2092941991, REVEL 0.02, MetaLR 0.04
- P6S (p.Pro6Ser), rs1320256969, ClinGen CA394283264, ClinVar RCV001755088, ClinVar RCV002488585, REVEL 0.07, MetaLR 0.07, Uncertain significance, PKD1-related disorder; Inborn genetic diseases; not provided
- A7T (p.Ala7Thr), rs1401224165, ClinGen CA394283245, ClinVar RCV002306080, gnomAD rs1401224165, REVEL 0.06, MetaLR 0.06, Uncertain significance, not provided
- R8H (p.Arg8His), TOPMed rs1366403752, REVEL 0.06, MetaLR 0.04
- R8L (p.Arg8Leu), TOPMed rs1366403752, REVEL 0.02, MetaLR 0.03
- L9M (p.Leu9Met), TOPMed rs926592294, gnomAD rs926592294, REVEL 0.04, MetaLR 0.05, Uncertain significance, Polycystic kidney disease, adult type
- A10V (p.Ala10Val), gnomAD rs2092941834, REVEL 0.04, MetaLR 0.03
- A12G (p.Ala12Gly), TOPMed rs1443010363, gnomAD rs1443010363, REVEL 0.04, MetaLR 0.04
- L13P (p.Leu13Pro), rs2092941758, ClinGen CA394283096, ClinVar RCV001289049, ClinVar RCV002486089, REVEL 0.24, MetaLR 0.09, Uncertain significance, not provided; Polycystic kidney disease, adult type
- L13Q (p.Leu13Gln), UniProt VAR 011030, MetaLR 0.08, MetaSVM -1.00, Pathogenic, in PKD1
- L13V (p.Leu13Val), rs982042024, ClinGen CA276756592, ClinVar RCV002779746, ClinVar RCV005011200, REVEL 0.05, MetaLR 0.05, Uncertain significance, Inborn genetic diseases; Polycystic kidney disease, adult type
- G16A (p.Gly16Ala), Ensembl rs2092941654, MetaLR 0.09, MetaSVM -1.03
- L19F (p.Leu19Phe), rs2151858362, ClinGen CA394282955, ClinVar RCV002267548, Ensembl rs2151858362, REVEL 0.01, MetaLR 0.04, Uncertain significance, not provided
- G20E (p.Gly20Glu), TOPMed rs2092941594, gnomAD rs2092941594, REVEL 0.17, MetaLR 0.07
- A21T (p.Ala21Thr), gnomAD rs2092941556, REVEL 0.02, MetaLR 0.04
- A23V (p.Ala23Val), TOPMed rs1026325632, gnomAD rs1026325632, REVEL 0.06, MetaLR 0.04, Uncertain significance, Polycystic kidney disease, adult type; Inborn genetic diseases; not provided
- G25C (p.Gly25Cys), TOPMed rs2092941472, REVEL 0.03, MetaLR 0.06
- G25R (p.Gly25Arg), TOPMed rs2092941472, REVEL 0.02, MetaLR 0.06
- G25S (p.Gly25Ser), TOPMed rs2092941472, REVEL 0.01, MetaLR 0.05
- G25V (p.Gly25Val), rs972049140, ClinGen CA276756583, ClinVar RCV000517600, ClinVar RCV001254275, REVEL 0.02, MetaLR 0.04, Benign
- P26L (p.Pro26Leu), Ensembl rs2151858338, REVEL 0.04, MetaLR 0.06
- G27A (p.Gly27Ala), 1000Genomes rs1596636820, gnomAD rs1596636820, REVEL 0.05, MetaLR 0.03
- R28C (p.Arg28Cys), TOPMed rs963532477, gnomAD rs963532477, REVEL 0.04, MetaLR 0.05, Uncertain significance, Polycystic kidney disease, adult type; not provided
- R28S (p.Arg28Ser), rs963532477, ClinGen CA394282830, ClinVar RCV003417581, REVEL 0.06, MetaLR 0.04, Uncertain significance, not provided
- G29A (p.Gly29Ala), TOPMed rs1798774818, MetaLR 0.04, MetaSVM -1.06
- C30Y (p.Cys30Tyr), rs2092941343, ClinGen CA394282797, ClinVar RCV001286026, Ensembl rs2092941343, REVEL 0.04, MetaLR 0.06, Uncertain significance, Polycystic kidney disease, adult type
- G31W (p.Gly31Trp), Ensembl rs2092941325, REVEL 0.03, MetaLR 0.05
- C33* (p.Cys33Ter), rs2092941253, ClinGen CA394282744, ClinVar RCV001095573, Ensembl rs2092941253, CADD 34.00, Pathogenic
- E34K (p.Glu34Lys), TOPMed rs1159090218
- P35H (p.Pro35His), TOPMed rs1007755475, gnomAD rs1007755475, REVEL 0.02, MetaLR 0.04
- P35L (p.Pro35Leu), TOPMed rs1007755475, gnomAD rs1007755475, REVEL 0.01, MetaLR 0.03, Uncertain significance, Inborn genetic diseases
- P35S (p.Pro35Ser), rs1016742393, ClinGen CA276756574, ClinVar RCV004506323, 1000Genomes rs1016742393, REVEL 0.01, MetaLR 0.05, Uncertain significance, Inborn genetic diseases
- P35T (p.Pro35Thr), 1000Genomes rs1016742393, TOPMed rs1016742393, gnomAD rs1016742393, REVEL 0.02, MetaLR 0.05, Uncertain significance
- P36A (p.Pro36Ala), TOPMed rs2092941107, gnomAD rs2092941107, REVEL 0.04, MetaLR 0.04
- P36H (p.Pro36His), rs560049593, ClinGen CA10587238, ClinVar RCV000755607, ClinVar RCV001254212, REVEL 0.08, MetaLR 0.06, Benign
- P36L (p.Pro36Leu), 1000Genomes rs560049593, TOPMed rs560049593, gnomAD rs560049593, REVEL 0.06, MetaLR 0.05, Benign
- P36S (p.Pro36Ser), TOPMed rs2092941107, gnomAD rs2092941107, REVEL 0.03, MetaLR 0.04
- C37* (p.Cys37Ter), rs2092941027, ClinGen CA394282677, ClinVar RCV001292448, ClinVar RCV003326560, CADD 34.00, Pathogenic
- C37A (p.Cys37Ala), NCI-TCGA TCGA novel, MetaLR 0.15, MetaSVM -0.99, Variant assessed as somatic; high impact.
- L38F (p.Leu38Phe), TOPMed rs1030433875, gnomAD rs1030433875, REVEL 0.01, MetaLR 0.03, Uncertain significance
- L38V (p.Leu38Val), rs1030433875, ClinGen CA276756563, ClinVar RCV001358432, ClinVar RCV003169775, REVEL 0.01, MetaLR 0.03, Uncertain significance, Inborn genetic diseases; not provided
- C39Y (p.Cys39Tyr), rs2151858290, ClinGen CA394282654, ClinVar RCV001767473, ClinVar RCV005006023, REVEL 0.21, MetaLR 0.16, Conflicting interpretations, not provided; Polycystic kidney disease, adult type
- P41A (p.Pro41Ala), TOPMed rs1318734922, gnomAD rs1318734922, REVEL 0.11, MetaLR 0.10, Uncertain significance
- P41L (p.Pro41Leu), gnomAD rs918687, REVEL 0.17, MetaLR 0.12
- P41S (p.Pro41Ser), TOPMed rs1318734922, gnomAD rs1318734922, REVEL 0.08, MetaLR 0.10, Uncertain significance, Polycystic kidney disease, adult type
- A42E (p.Ala42Glu), TOPMed rs1242983545, gnomAD rs1242983545, REVEL 0.07, MetaLR 0.08
- A42T (p.Ala42Thr), TOPMed rs2092940852, REVEL 0.06, MetaLR 0.07
- A42V (p.Ala42Val), TOPMed rs1242983545, gnomAD rs1242983545, REVEL 0.06, MetaLR 0.07
- P43A (p.Pro43Ala), rs1114167365, ClinGen CA394282577, ClinVar RCV000490643, TOPMed rs1114167365, REVEL 0.05, MetaLR 0.08, Polycystic kidney disease, adult type
- P43L (p.Pro43Leu), TOPMed rs2092940762, REVEL 0.07, MetaLR 0.09
- A45V (p.Ala45Val), gnomAD rs2092940705, REVEL 0.04, MetaLR 0.05
- A46T (p.Ala46Thr), TOPMed rs2092940675, REVEL 0.02, MetaLR 0.05
- C47R (p.Cys47Arg), TOPMed rs2092940626, REVEL 0.25, MetaLR 0.10
- V49I (p.Val49Ile), Ensembl rs2092940602, REVEL 0.13, MetaLR 0.12
- N50S (p.Asn50Ser), gnomAD rs1315364389, REVEL 0.05, MetaLR 0.05, Uncertain significance, Polycystic kidney disease, adult type
- C51G (p.Cys51Gly), rs2151858256, ClinGen CA394282413, ClinVar RCV002267544, ClinVar RCV005397354, Uncertain significance, not provided; Polycystic kidney disease, adult type
- C51R (p.Cys51Arg), rs2151858256, ClinGen CA394282414, ClinVar RCV003127115, Uncertain significance, not provided
- C51S (p.Cys51Ser), rs2151858256, ClinGen CA394282416, ClinVar RCV003991101, Likely pathogenic, Polycystic kidney disease, adult type
- S52* (p.Ser52Ter), rs2092940490, ClinGen CA394282394, ClinVar RCV003236130, CADD 36.00, Pathogenic
- S52P (p.Ser52Pro), rs2544960233, ClinGen CA394282397, ClinVar RCV003976879, REVEL 0.20, MetaLR 0.07, Uncertain significance, PKD1-related disorder
- S52W (p.Ser52Trp), rs2092940490, ClinGen CA394282392, ClinVar RCV001092721, Ensembl rs2092940490, REVEL 0.27, MetaLR 0.12, Likely pathogenic
- G53A (p.Gly53Ala), rs2544960223, ClinGen CA394282380, ClinVar RCV002284827, Uncertain significance, not specified; not provided
- R54G (p.Arg54Gly), TOPMed rs1053936081, gnomAD rs1053936081, REVEL 0.05, MetaLR 0.05, Uncertain significance, Inborn genetic diseases; Polycystic kidney disease, adult type
- R54S (p.Arg54Ser), TOPMed rs1053936081, gnomAD rs1053936081, REVEL 0.07, MetaLR 0.04, Uncertain significance
- G55R (p.Gly55Arg), TOPMed rs1466702158, REVEL 0.06, MetaLR 0.08, Uncertain significance, not specified
- L56P (p.Leu56Pro), rs2092940195, ClinGen CA394282329, ClinVar RCV001254307, ClinVar RCV001292022, REVEL 0.16, MetaLR 0.12, Uncertain significance, Inborn genetic diseases; Autosomal dominant polycystic kidney disease
- L56V (p.Leu56Val), Ensembl rs2092940218, REVEL 0.06, MetaLR 0.10
- R57W (p.Arg57Trp), rs1315029199, ClinGen CA394282321, ClinVar RCV003268388, ClinVar RCV005021892, REVEL 0.13, MetaLR 0.06, Uncertain significance, Inborn genetic diseases; Polycystic kidney disease, adult type
- T58M (p.Thr58Met), TOPMed rs937748491, gnomAD rs937748491, REVEL 0.04, MetaLR 0.04
- T58R (p.Thr58Arg), TOPMed rs937748491, gnomAD rs937748491, REVEL 0.02, MetaLR 0.03
- P61L (p.Pro61Leu), rs886038369, ClinGen CA10587237, ClinVar RCV000245926, ClinVar RCV000712592, REVEL 0.08, MetaLR 0.09, Benign, in PKD1
- L63V (p.Leu63Val), gnomAD rs1346962118, REVEL 0.12, MetaLR 0.07
- R64H (p.Arg64His), TOPMed rs1300272809, REVEL 0.09, MetaLR 0.07, Uncertain significance
- R64P (p.Arg64Pro), rs1300272809, ClinGen CA394282229, ClinVar RCV002293271, TOPMed rs1300272809, REVEL 0.07, MetaLR 0.05, Uncertain significance, Polycystic kidney disease, adult type
- D68E (p.Asp68Glu), TOPMed rs2092939906, REVEL 0.20, MetaLR 0.47
- D68N (p.Asp68Asn), Ensembl rs2092939926, MetaLR 0.47, MetaSVM -0.73
- A69T (p.Ala69Thr), TOPMed rs1205227733, REVEL 0.23, MetaLR 0.28
- A69V (p.Ala69Val), rs2151858171, ClinGen CA394282155, ClinVar RCV001354318, Ensembl rs2151858171, REVEL 0.23, MetaLR 0.25, Uncertain significance, not provided
- A71E (p.Ala71Glu), TOPMed rs1365988821, gnomAD rs1365988821, REVEL 0.08, MetaLR 0.07
- A71S (p.Ala71Ser), TOPMed rs1423829809, gnomAD rs1423829809, REVEL 0.09, MetaLR 0.06
- A71V (p.Ala71Val), TOPMed rs1365988821, gnomAD rs1365988821, REVEL 0.03, MetaLR 0.05
- L72Q (p.Leu72Gln), rs1596636573, ClinGen CA394282123, ClinVar RCV001029930, Ensembl rs1596636573, Uncertain significance
- L72V (p.Leu72Val), 1000Genomes rs972113626, gnomAD rs972113626, REVEL 0.38, MetaLR 0.84, Benign
- D73G (p.Asp73Gly), rs2151826654, ClinGen CA394396333, ClinVar RCV001795812, ClinVar RCV006269478, REVEL 0.63, MetaLR 0.82, Uncertain significance, not specified; Polycystic kidney disease, adult type
- V74I (p.Val74Ile), rs1048339818, ClinGen CA276784283, ClinVar RCV003376394, TOPMed rs1048339818, REVEL 0.03, MetaLR 0.07, Likely benign, Inborn genetic diseases; not provided
- V74L (p.Val74Leu), TOPMed rs1048339818, gnomAD rs1048339818, REVEL 0.04, MetaLR 0.01, Likely benign
- S75F (p.Ser75Phe), UniProt VAR 011031, REVEL 0.74, MetaLR 0.87, Likely pathogenic, Polycystic kidney disease, adult type
- S75Y (p.Ser75Tyr), rs2544886187, ClinVar RCV004595038, REVEL 0.68, MetaLR 0.86, Uncertain significance, Polycystic kidney disease, adult type
- H76Y (p.His76Tyr), rs932577597, ClinGen CA276784281, cosmic curated COSV51917, ClinVar RCV000626721, REVEL 0.11, MetaLR 0.10, Uncertain significance
- N77S (p.Asn77Ser), rs2092686792, ClinGen CA394396304, ClinVar RCV001758197, ClinVar RCV005006008, REVEL 0.41, MetaLR 0.60, Conflicting interpretations, not specified; Polycystic kidney disease, adult type; not provided
- R80Q (p.Arg80Gln), rs1190107349, ClinGen CA394396275, ClinVar RCV000712601, TOPMed rs1190107349, REVEL 0.04, MetaLR 0.08, Uncertain significance
- R80W (p.Arg80Trp), rs551353498, ClinGen CA7833767, cosmic curated COSV51909, ClinVar RCV000712600, REVEL 0.12, MetaLR 0.25, Benign
- A81V (p.Ala81Val), rs531570028, ClinGen CA7833766, ClinVar RCV003981761, ClinVar RCV005419748, REVEL 0.10, MetaLR 0.05, Likely benign, not specified; Inborn genetic diseases
- V84F (p.Val84Phe), TOPMed rs914018183, gnomAD rs914018183, REVEL 0.05, MetaLR 0.12, Likely benign
- V84I (p.Val84Ile), rs914018183, ClinGen CA276784276, cosmic curated COSV51919, ClinVar RCV003426523, REVEL 0.02, MetaLR 0.08, Conflicting interpretations, not provided; Polycystic kidney disease, adult type
- G85V (p.Gly85Val), Ensembl rs1828076954, REVEL 0.19, MetaLR 0.25
- L86F (p.Leu86Phe), TOPMed rs1263493445, gnomAD rs1263493445, REVEL 0.04, MetaLR 0.09
- L87M (p.Leu87Met), UniProt VAR 058761, REVEL 0.22, MetaLR 0.30
- A88P (p.Ala88Pro), TOPMed rs988615072
- A88T (p.Ala88Thr), TOPMed rs988615072
- A88V (p.Ala88Val), rs958271752, ClinGen CA276784272, NCI-TCGA Cosmic COSV9923, cosmic curated COSV99238, REVEL 0.03, MetaLR 0.12, Conflicting interpretations, Inborn genetic diseases; Polycystic kidney disease, adult type
- N89D (p.Asn89Asp), rs1287585087, ClinGen CA394396193, ClinVar RCV003899175, ClinVar RCV005455908, REVEL 0.09, MetaLR 0.19, Uncertain significance, Inborn genetic diseases
- N89K (p.Asn89Lys), TOPMed rs1596593651, MetaLR 0.19, MetaSVM -0.91
- N89T (p.Asn89Thr), rs1434978033, ClinGen CA394396190, ClinVar RCV004506361, TOPMed rs1434978033, REVEL 0.08, MetaLR 0.20, Uncertain significance, Inborn genetic diseases
- L90F (p.Leu90Phe), ExAC rs760560538, TOPMed rs760560538, gnomAD rs760560538, REVEL 0.23, MetaLR 0.46
- S91* (p.Ser91Ter), rs1339097856, ClinGen CA394396164, ClinVar RCV001535930, 1000Genomes rs1339097856, Pathogenic
- S91A (p.Ser91Ala), TOPMed rs1167450317
- S91L (p.Ser91Leu), rs1339097856, ClinGen CA394396161, ClinVar RCV002763631, 1000Genomes rs1339097856, REVEL 0.14, MetaLR 0.20, Uncertain significance, Inborn genetic diseases
- A92V (p.Ala92Val), gnomAD rs1375510281, REVEL 0.03, MetaLR 0.10
- L93P (p.Leu93Pro), rs2151826530, ClinGen CA394396143, ClinVar RCV001844984, Ensembl rs2151826530, Likely pathogenic, Autosomal dominant polycystic kidney disease
- A94V (p.Ala94Val), TOPMed rs1428551004, gnomAD rs1428551004, REVEL 0.03, MetaLR 0.07
- E95D (p.Glu95Asp), rs1305213807, ClinGen CA394396119, ClinVar RCV000788678, ClinVar RCV005012313, REVEL 0.06, MetaLR 0.17, Uncertain significance, PKD1-related disorder
- D97G (p.Asp97Gly), rs2092684310, ClinGen CA394396068, ClinVar RCV001293852, UniProt VAR 064380, Likely pathogenic, Polycystic kidney disease, adult type
- D97N (p.Asp97Asn), NCI-TCGA TCGA novel, REVEL 0.08, MetaLR 0.13, Variant assessed as somatic; moderate impact., in PKD1
- I98V (p.Ile98Val), ExAC rs764218106, gnomAD rs764218106, REVEL 0.05, MetaLR 0.11, Uncertain significance, Inborn genetic diseases
- S99I (p.Ser99Ile), rs1567219544, ClinGen CA394396049, ClinVar RCV000788849, ClinVar RCV003413585, Uncertain significance, in PKD1
- S99N (p.Ser99Asn), Ensembl rs1567219544, REVEL 0.19, MetaLR 0.39, Uncertain significance, in PKD1
- S99R (p.Ser99Arg), ExAC rs762952101, gnomAD rs762952101, REVEL 0.34, MetaLR 0.37, Uncertain significance, Polycystic kidney disease, adult type
- N100D (p.Asn100Asp), gnomAD rs1159543723, REVEL 0.07, MetaLR 0.18
- N100S (p.Asn100Ser), gnomAD rs1420665040, REVEL 0.07, MetaLR 0.20
- N101D (p.Asn101Asp), rs2092684149, ClinGen CA394396026, ClinVar RCV001095576, ClinVar RCV001292325, REVEL 0.80, MetaLR 0.96, Uncertain significance
- N101K (p.Asn101Lys), rs2092684130, ClinGen CA394396015, ClinVar RCV001198548, ClinVar RCV001751364, REVEL 0.74, MetaLR 0.96, Uncertain significance, not provided; Polycystic kidney disease, adult type; not specified
- K102* (p.Lys102Ter), rs2092684104, ClinGen CA394396009, ClinVar RCV001292014, ClinVar RCV006249740, Pathogenic
- I103S (p.Ile103Ser), ExAC rs775619020, REVEL 0.52, MetaLR 0.46
- S104P (p.Ser104Pro), Ensembl rs200463151, REVEL 0.22, MetaLR 0.37, Uncertain significance, Polycystic kidney disease, adult type
- T105A (p.Thr105Ala), 1000Genomes rs200420603, ExAC rs200420603, TOPMed rs200420603, gnomAD rs200420603, REVEL 0.12, MetaLR 0.12, Likely benign
- T105M (p.Thr105Met), ExAC rs759844373, TOPMed rs759844373, gnomAD rs759844373, REVEL 0.21, MetaLR 0.30
- T105R (p.Thr105Arg), ExAC rs759844373, TOPMed rs759844373, gnomAD rs759844373, MetaLR 0.28, MetaSVM -0.47
- T105S (p.Thr105Ser), rs200420603, ClinGen CA7833740, ClinVar RCV002960333, ClinVar RCV003332415, REVEL 0.09, MetaLR 0.09, Conflicting interpretations, Inborn genetic diseases; not provided
- E107D (p.Glu107Asp), NCI-TCGA TCGA novel, MetaLR 0.31, MetaSVM -0.41, Variant assessed as somatic; moderate impact.
- E107K (p.Glu107Lys), Ensembl rs1355372612, REVEL 0.21, MetaLR 0.34, Uncertain significance, Inborn genetic diseases
- E108* (p.Glu108Ter), rs1416011785, ClinGen CA394395947, ClinVar RCV001029912, TOPMed rs1416011785, Pathogenic
- E108G (p.Glu108Gly), ExAC rs747538499, gnomAD rs747538499, REVEL 0.29, MetaLR 0.26
- E108K (p.Glu108Lys), TOPMed rs1416011785, REVEL 0.31, MetaLR 0.26, Pathogenic
- E108Q (p.Glu108Gln), TOPMed rs1416011785, MetaLR 0.17, MetaSVM -0.78, Pathogenic
- G109E (p.Gly109Glu), ExAC rs778158409, TOPMed rs778158409, gnomAD rs778158409, REVEL 0.20, MetaLR 0.16, Uncertain significance, Inborn genetic diseases
- G109R (p.Gly109Arg), Ensembl rs2092683833, REVEL 0.29, MetaLR 0.26
- I110L (p.Ile110Leu), NCI-TCGA Cosmic COSV5191, cosmic curated COSV51918, MetaLR 0.05, MetaSVM -1.05, Variant assessed as somatic; moderate impact.
- I110M (p.Ile110Met), TOPMed rs2092683766, REVEL 0.04, MetaLR 0.13, Uncertain significance, Polycystic kidney disease, adult type
- F111L (p.Phe111Leu), TOPMed rs1238545476, gnomAD rs1238545476, REVEL 0.28, MetaLR 0.27
- A112G (p.Ala112Gly), rs1261496619, ClinGen CA394395898, ClinVar RCV003319664, Uncertain significance, not provided
- A112T (p.Ala112Thr), gnomAD rs1241541582, REVEL 0.02, MetaLR 0.08
- A112V (p.Ala112Val), TOPMed rs1261496619, gnomAD rs1261496619, REVEL 0.05, MetaLR 0.12, Uncertain significance, Inborn genetic diseases
- N113D (p.Asn113Asp), TOPMed rs1356177978, REVEL 0.04, MetaLR 0.19
- N113H (p.Asn113His), TOPMed rs1356177978
- N113S (p.Asn113Ser), TOPMed rs1315541372, gnomAD rs1315541372, REVEL 0.06, MetaLR 0.10
- L114V (p.Leu114Val), rs980956715, ClinGen CA276784215, ClinVar RCV003990449, TOPMed rs980956715, REVEL 0.42, MetaLR 0.56, Uncertain significance, Polycystic kidney disease, adult type
- F115L (p.Phe115Leu), gnomAD rs1408818434, REVEL 0.04, MetaLR 0.08
- L117F (p.Leu117Phe), NCI-TCGA TCGA novel, Variant assessed as somatic; moderate impact.
- S118G (p.Ser118Gly), TOPMed rs969529348, gnomAD rs969529348, REVEL 0.18, MetaLR 0.36, Uncertain significance, Polycystic kidney disease, adult type
- S118N (p.Ser118Asn), gnomAD rs1267295455, MetaLR 0.28, MetaSVM -0.36
- S118T (p.Ser118Thr), gnomAD rs1267295455, REVEL 0.11, MetaLR 0.18
- E119G (p.Glu119Gly), ExAC rs748839748, gnomAD rs748839748, REVEL 0.11, MetaLR 0.22
- E119K (p.Glu119Lys), TOPMed rs1248093078, REVEL 0.04, MetaLR 0.15, Uncertain significance, Polycystic kidney disease, adult type; Inborn genetic diseases
- I120T (p.Ile120Thr), rs1555459345, ClinGen CA394395810, ClinVar RCV000626722, ClinVar RCV003162769, REVEL 0.35, MetaLR 0.18, Likely pathogenic
- I120V (p.Ile120Val), TOPMed rs2092683472
- L122M (p.Leu122Met), 1000Genomes rs551684367, ExAC rs551684367, gnomAD rs551684367, REVEL 0.69, MetaLR 0.89
- S123T (p.Ser123Thr), ExAC rs748717453, TOPMed rs748717453, gnomAD rs748717453, REVEL 0.21, MetaLR 0.29
- G124V (p.Gly124Val), NCI-TCGA TCGA novel, Variant assessed as somatic; moderate impact.
- G124W (p.Gly124Trp), ExAC rs779681895, gnomAD rs779681895
- P126L (p.Pro126Leu), rs1567219166, ClinGen CA394395695, ClinVar RCV000785951, TOPMed rs1567219166, REVEL 0.74, MetaLR 0.79, Uncertain significance
- P126R (p.Pro126Arg), NCI-TCGA TCGA novel, MetaLR 0.69, MetaSVM 0.67, Variant assessed as somatic; moderate impact.
- F127C (p.Phe127Cys), rs2092679766, ClinGen CA394395686, ClinVar RCV001281205, Ensembl rs2092679766, Likely pathogenic, Polycystic kidney disease, adult type
- E128* (p.Glu128Ter), rs2544883301, ClinVar RCV004556961, ClinVar RCV006264312, CADD 36.00, Pathogenic
- E128V (p.Glu128Val), gnomAD rs2092679750, REVEL 0.17, MetaLR 0.43
- D130E (p.Asp130Glu), TOPMed rs1300136928, gnomAD rs1300136928, REVEL 0.52, MetaLR 0.72
- G132A (p.Gly132Ala), TOPMed rs1353418836, gnomAD rs1353418836, REVEL 0.23, MetaLR 0.46
- L133V (p.Leu133Val), TOPMed rs1414167872, gnomAD rs1414167872, REVEL 0.48, MetaLR 0.79
- A134T (p.Ala134Thr), gnomAD rs1362871350, REVEL 0.16, MetaLR 0.54
- A134V (p.Ala134Val), rs1296786347, ClinGen CA394395615, ClinVar RCV003977112, ClinVar RCV005707282, REVEL 0.10, MetaLR 0.39, Likely benign, Inborn genetic diseases
- W135* (p.Trp135Ter), rs1567219111, ClinGen CA394395603, ClinVar RCV000735699, Ensembl rs1567219111, CADD 36.00, Pathogenic
- W135C (p.Trp135Cys), rs2092679535, ClinGen CA394395594, ClinVar RCV001289051, ClinVar RCV002499508, REVEL 0.79, MetaLR 0.89, Uncertain significance, not provided; Polycystic kidney disease, adult type
- L136Q (p.Leu136Gln), rs2544883206, ClinGen CA394395586, ClinVar RCV002289352, Uncertain significance, Polycystic kidney disease, adult type
- P137L (p.Pro137Leu), rs531501851, ClinGen CA7833711, ClinVar RCV003981557, 1000Genomes rs531501851, REVEL 0.31, MetaLR 0.47, Likely benign, PKD1-related disorder
- P137Q (p.Pro137Gln), 1000Genomes rs531501851, ExAC rs531501851, TOPMed rs531501851, gnomAD rs531501851, REVEL 0.38, MetaLR 0.71, Likely benign
Public PKD1 analysis runs
- PKD1 analysis run — PKD1 (7,773 variants) — completed 2026-08-18