CACNA1A (O00555) variants and mutations

CACNA1A (also known as O00555) is a human protein-coding gene encoding a voltage-dependent P/Q-type calcium channel subunit alpha-1A protein. Its P/Q-type calcium current is a major trigger for neurotransmitter release at central synapses and is especially important in cerebellar circuits. Pathogenic variants cause a spectrum including familial hemiplegic migraine, episodic ataxia, spinocerebellar ataxia type 6, epilepsy, and developmental disorders. This analysis covers 4,079 CACNA1A variants and mutations. Of these, 86% have computational variant effect predictions. Disease context includes Familial paroxysmal ataxia, episodic ataxia type 2, and migraine, familial hemiplegic, 1. Example CACNA1A variants include A2S, A2V, and R3C.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.

Notable CACNA1A variants

Examples include A2S, A2V, R3C, R3G, R3H, G5V, D6E, E7K. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.