ACVR1 (Activin receptor type-1) variants and mutations

ACVR1 (also known as Activin receptor type-1) is a human protein-coding gene encoding an activin receptor type-1 protein. It transduces BMP-family signals that regulate bone formation and developmental patterning. Recurrent activating variants cause fibrodysplasia ossificans progressiva by making connective-tissue cells abnormally responsive to osteogenic signaling, and somatic variants also occur in diffuse midline glioma. This analysis covers 875 ACVR1 variants and mutations. Of these, 68% have computational variant effect predictions. Disease context includes fibrodysplasia ossificans progressiva, myelofibrosis, and neoplasm. Example ACVR1 variants include M1?, M1V, and V2I.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.

Notable ACVR1 variants

Examples include M1?, M1V, V2I, D3Y, G4E, G4R, V5M, M6V. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.