TAFAZZIN (Q16635) variants and mutations
TAFAZZIN (also known as Q16635) is a human protein-coding gene encoding a tafazzin protein. It remodels mitochondrial cardiolipin so the inner mitochondrial membrane can support efficient respiratory-chain organization and energy production. Loss-of-function variants cause Barth syndrome, characterized by cardiomyopathy, skeletal myopathy, neutropenia, growth delay, and abnormal cardiolipin composition. This analysis covers 479 TAFAZZIN variants and mutations. Of these, 71% have computational variant effect predictions. Disease context includes Barth syndrome, dilated cardiomyopathy, and Abnormality of the cardiovascular system. Example TAFAZZIN variants include M1I, M1V, and P2H.
Variant analysis overview
- Gene: TAFAZZIN
- Protein: Q16635
- UniProt accession: Q16635
- Organism: Homo sapiens
- Variants analyzed: 479
- Variant scope: all variants
- Completed: 2026-08-19
Variant and mutation evidence
- Variant composition: 279 unspecified-consequence records; 112 missense variants; 71 synonymous variants; 4 stop-gained variants; 6 splice-region variants; 5 frameshift variants; 2 in-frame deletions
- Prediction scores: 339 variants have prediction scores (71% of the analyzed set).
Clinical, disease, and population context
- Disease context: 25 disease associations are represented. Top associations: Barth syndrome, dilated cardiomyopathy, Abnormality of the cardiovascular system, cardiomyopathy, familial isolated dilated cardiomyopathy, Left ventricular noncompaction cardiomyopathy, endocardial fibroelastosis, gastric carcinoma, familial dilated cardiomyopathy, left ventricular noncompaction, dilated cardiomyopathy 1A, familial hypertrophic cardiomyopathy.
Data sources
Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, AlphaFold DB, gnomAD constraint, Open Targets, MaveDB, LitVar.
Notable TAFAZZIN variants
Examples include M1I, M1V, P2H, P2T, L3M, L3L, H4Q, H4Y. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.
- M1I (p.Met1Ile), rs2522918261, ClinGen CA415177854, ClinVar RCV002881106, Uncertain significance, 3-Methylglutaconic aciduria type 2
- M1V (p.Met1Val), rs12845698, ClinGen CA415177839, ClinVar RCV002929157, MetaLR 0.97, MetaSVM 1.10, Uncertain significance, 3-Methylglutaconic aciduria type 2
- P2H (p.Pro2His), Ensembl rs1557190766, CADD 24.80, PolyPhen-2 1.00
- P2T (p.Pro2Thr), gnomAD X-154411847-C-A, CADD 23.80, PolyPhen-2 1.00
- L3M (p.Leu3Met), 1000Genomes rs2148184240, CADD 24.00, PolyPhen-2 1.00
- L3L (p.Leu3Leu), gnomAD X-154411850-C-T, CADD 12.40
- H4Q (p.His4Gln), ExAC rs782329160, TOPMed rs782329160, gnomAD rs782329160, CADD 5.57, PolyPhen-2 0.02
- H4Y (p.His4Tyr), gnomAD rs1557190780, CADD 16.90, PolyPhen-2 0.43, Uncertain significance, 3-Methylglutaconic aciduria type 2
- H4N (p.His4Asn), gnomAD X-154411853-C-A, CADD 9.24, PolyPhen-2 0.27
- H4R (p.His4Arg), gnomAD X-154411854-A-G, CADD 13.00, PolyPhen-2 0.16
- V5L (p.Val5Leu), rs397515737, ClinGen CA131101, ClinVar RCV000035086, ClinVar RCV000766522, CADD 25.80, PolyPhen-2 0.98, Uncertain significance
- V5M (p.Val5Met), gnomAD X-154411856-G-A, CADD 26.40, PolyPhen-2 0.99
- V5V (p.Val5Val), gnomAD X-154411858-G-T, CADD 14.50
- K6N (p.Lys6Asn), rs782245384, ClinGen CA10562255, ClinVar RCV002613639, ExAC rs782245384, CADD 18.30, PolyPhen-2 0.99, Uncertain significance, 3-Methylglutaconic aciduria type 2
- K6T (p.Lys6Thr), gnomAD X-154411860-A-C, CADD 22.90, PolyPhen-2 0.99
- K6K (p.Lys6Lys), gnomAD X-154411861-G-A, CADD 9.49
- K6* (p.Lys6Ter), rs1557191627, gnomAD X-154413275-A-T, CADD 4.95
- W7C (p.Trp7Cys), cosmic curated COSV50010, ExAC rs781958696, gnomAD rs781958696, CADD 32.00, PolyPhen-2 1.00
- W7S (p.Trp7Ser), ExAC rs782387580
- W7L (p.Trp7Leu), gnomAD X-154411863-G-T, CADD 28.60, PolyPhen-2 0.99
- W7* (p.Trp7Ter), gnomAD X-154411864-G-A, CADD 35.00
- W7R (p.Trp7Arg), gnomAD X-154413278-T-A, CADD 9.22
- P8L (p.Pro8Leu), gnomAD rs1557190811, CADD 24.20, PolyPhen-2 1.00
- P8S (p.Pro8Ser), ExAC rs782099548, gnomAD rs782099548, CADD 24.00, PolyPhen-2 1.00
- P8Q (p.Pro8Gln), gnomAD X-154411866-C-A, CADD 25.90, PolyPhen-2 1.00
- P8P (p.Pro8Pro), rs2068311070, gnomAD X-154411867-G-A, CADD 14.20
- P8T (p.Pro8Thr), gnomAD X-154418551-C-A, CADD 1.36, SIFT 0.61
- F9L (p.Phe9Leu), rs1223065368, ClinGen CA415178018, ClinVar RCV001042821, ClinVar RCV002462272, CADD 24.00, PolyPhen-2 0.95, Conflicting interpretations, 3-Methylglutaconic aciduria type 2; Cardiovascular phenotype
- F9V (p.Phe9Val), gnomAD X-154411868-T-G, CADD 27.00, PolyPhen-2 0.97
- F9Y (p.Phe9Tyr), gnomAD X-154411869-T-A, CADD 27.00, PolyPhen-2 0.95
- F9F (p.Phe9Phe), gnomAD X-154411870-C-T, CADD 15.50
- F9S (p.Phe9Ser), gnomAD X-154418558-T-C, CADD 2.54, SIFT 0.42
- P10R (p.Pro10Arg), rs781941217, ClinGen CA10562260, ClinVar RCV000853160, ClinVar RCV001169982, CADD 26.00, PolyPhen-2 1.00, Uncertain significance, Left ventricular noncompaction cardiomyopathy; 3-Methylglutaconic aciduria type
- P10S (p.Pro10Ser), rs782316788, ClinGen CA10562259, ClinVar RCV003825311, ExAC rs782316788, CADD 25.80, PolyPhen-2 1.00, Uncertain significance, 3-Methylglutaconic aciduria type 2
- P10T (p.Pro10Thr), gnomAD X-154411871-C-A, CADD 25.50, PolyPhen-2 1.00
- P10P (p.Pro10Pro), gnomAD X-154411873-C-A, CADD 10.70
- A11S (p.Ala11Ser), cosmic curated COSV10583, CADD 16.50, PolyPhen-2 0.99
- A11V (p.Ala11Val), cosmic curated COSV10955, gnomAD rs1557190828, CADD 19.50, PolyPhen-2 0.99
- A11T (p.Ala11Thr), gnomAD X-154411874-G-A, CADD 18.50, PolyPhen-2 0.99
- A11E (p.Ala11Glu), gnomAD X-154411875-C-A, CADD 15.80, PolyPhen-2 1.00
- A11A (p.Ala11Ala), rs782158312, gnomAD X-154411876-G-C, CADD 8.39
- A11P (p.Ala11Pro), gnomAD X-154413299-G-C, CADD 0.52
- V12L (p.Val12Leu), gnomAD X-154411877-G-T, CADD 22.20, PolyPhen-2 0.97
- V12V (p.Val12Val), gnomAD X-154411879-G-T, CADD 12.90
- P13L (p.Pro13Leu), gnomAD rs1557190859, CADD 26.20, PolyPhen-2 1.00
- P13R (p.Pro13Arg), gnomAD rs1557190859, CADD 24.10, PolyPhen-2 1.00
- P13S (p.Pro13Ser), rs1557190850, ClinGen CA415178060, ClinVar RCV002463268, ClinVar RCV003512187, CADD 25.20, PolyPhen-2 1.00, Uncertain significance, 3-Methylglutaconic aciduria type 2; Cardiovascular phenotype
- P13P (p.Pro13Pro), rs1557190864, gnomAD X-154411882-G-A, CADD 14.10
- P14Q (p.Pro14Gln), rs2522919267, ClinGen CA415178142, ClinVar RCV002300862, CADD 18.00, PolyPhen-2 0.49, Uncertain significance, not provided
- P14S (p.Pro14Ser), gnomAD X-154411883-C-T, CADD 16.40, PolyPhen-2 0.26
- P14R (p.Pro14Arg), gnomAD X-154411884-C-G, CADD 13.70, PolyPhen-2 0.01
- P14P (p.Pro14Pro), gnomAD X-154411885-G-C, CADD 13.20
- P21del (p.Pro21del), gnomAD X-154413316-CCCT-, CADD 9.22
- P14L (p.Pro14Leu), rs782476453, gnomAD X-154413318-C-T, CADD 7.16
- L15I (p.Leu15Ile), gnomAD X-154411886-C-A, CADD 19.10, PolyPhen-2 0.03
- L15L (p.Leu15Leu), gnomAD X-154411888-C-A, CADD 17.10
- T16I (p.Thr16Ile), TOPMed rs1227132566, AlphaMissense 0.10, MetaLR 0.87, Uncertain significance
- T16S (p.Thr16Ser), rs1227132566, ClinGen CA415178178, ClinVar RCV001228815, TOPMed rs1227132566, AlphaMissense 0.10, MetaLR 0.87, Uncertain significance, 3-Methylglutaconic aciduria type 2
- T16T (p.Thr16Thr), rs397515743, gnomAD X-154411891-C-G, CADD 21.00
- W17* (p.Trp17Ter), rs1603376560, ClinGen CA415178215, ClinVar RCV003237270, AlphaMissense 0.96, MetaLR 0.98, Likely pathogenic
- W17C (p.Trp17Cys), rs1603376560, ClinGen CA415178217, ClinVar RCV000813199, Ensembl rs1603376560, AlphaMissense 0.96, MetaLR 0.98, Uncertain significance, 3-Methylglutaconic aciduria type 2
- W17L (p.Trp17Leu), Ensembl rs868907951
- W17R (p.Trp17Arg), rs2068313278, ClinGen CA415178196, ClinVar RCV001167554, ClinVar RCV001167555, AlphaMissense 0.96, MetaLR 0.96, Uncertain significance, Endocardial fibroelastosis; 3-Methylglutaconic aciduria type 2; Primary dilated
- W17G (p.Trp17Gly), gnomAD X-154411892-T-G, CADD 25.90, PolyPhen-2 0.99
- T18I (p.Thr18Ile), rs2522919623, ClinGen CA415178225, ClinVar RCV003513406, CADD 23.00, PolyPhen-2 0.99, Uncertain significance, 3-Methylglutaconic aciduria type 2
- T18T (p.Thr18Thr), rs781846964, gnomAD X-154411897-C-T, CADD 13.50
- L19M (p.Leu19Met), TOPMed rs1327665804, gnomAD rs1327665804, CADD 24.50, PolyPhen-2 1.00, Likely benign
- L19L (p.Leu19Leu), rs1327665804, gnomAD X-154411898-C-T, CADD 14.50
- L19F (p.Leu19Phe), gnomAD X-154418587-C-T, CADD 6.00, SIFT 0.69
- A20S (p.Ala20Ser), gnomAD X-154411901-G-T, CADD 24.10, PolyPhen-2 0.98
- A20A (p.Ala20Ala), gnomAD X-154411903-C-T, CADD 16.60
- S21I (p.Ser21Ile), Ensembl rs112148852, CADD 28.30, PolyPhen-2 0.99
- S21L (p.Ser21Leu), rs368429047, gnomAD X-154413273-C-T, CADD 5.39
- S21W (p.Ser21Trp), gnomAD X-154413273-C-G, CADD 4.91
- S21S (p.Ser21Ser), rs782727666, gnomAD X-154413274-G-A, CADD 1.08
- S21F (p.Ser21Phe), gnomAD X-154418549-C-T, CADD 3.61, SIFT 0.72
- S21R (p.Ser21Arg), rs1557193530, gnomAD X-154418574-C-A, CADD 2.62, SIFT 0.45
- S22N (p.Ser22Asn), NCI-TCGA Cosmic COSV5001, cosmic curated COSV50010, Variant assessed as somatic; moderate impact.
- S22G (p.Ser22Gly), gnomAD X-154411907-A-G, CADD 24.30, PolyPhen-2 0.95
- S22S (p.Ser22Ser), gnomAD X-154411909-C-T, CADD 13.30
- V23I (p.Val23Ile), rs2522919882, ClinGen CA415178339, ClinVar RCV002460783, cosmic curated COSV50010, Uncertain significance, Cardiovascular phenotype
- V23V (p.Val23Val), rs782123597, gnomAD X-154411912-C-T, CADD 15.40
- V24I (p.Val24Ile), rs1557190907, gnomAD rs1557190907, CADD 23.60, PolyPhen-2 0.97, Variant assessed as somatic; moderate impact.
- G26C (p.Gly26Cys), gnomAD X-154411919-G-T, CADD 26.10, PolyPhen-2 1.00
- G26A (p.Gly26Ala), gnomAD X-154413283-CGG-C, CADD 0.36
- G26R (p.Gly26Arg), rs376540475, gnomAD X-154413284-G-A, CADD 0.27
- G26W (p.Gly26Trp), rs376540475, gnomAD X-154413284-G-T, CADD 0.22
- G26E (p.Gly26Glu), gnomAD X-154413285-G-A, CADD 0.81
- G26G (p.Gly26Gly), gnomAD X-154413286-G-A, CADD 7.37
- G26V (p.Gly26Val), gnomAD X-154418555-G-T, CADD 3.38, SIFT 0.61
- L27L (p.Leu27Leu), rs782716787, gnomAD X-154411922-T-C, CADD 14.10
- L27F (p.Leu27Phe), gnomAD X-154411924-G-T, CADD 22.40, PolyPhen-2 0.99
- V28L (p.Val28Leu), gnomAD X-154411925-G-T, CADD 26.90, PolyPhen-2 0.97
- G29R (p.Gly29Arg), rs2522920099, ClinGen CA415178487, ClinVar RCV003512726, ClinVar RCV004780595, Uncertain significance, 3-Methylglutaconic aciduria type 2; not provided
- G29C (p.Gly29Cys), gnomAD X-154411928-G-T, CADD 32.00, PolyPhen-2 1.00
- T30I (p.Thr30Ile), rs2068315101, ClinGen CA415178519, ClinVar RCV001051674, Ensembl rs2068315101, AlphaMissense 0.80, MetaLR 0.93, Uncertain significance, 3-Methylglutaconic aciduria type 2
- T30T (p.Thr30Thr), rs1557190917, gnomAD X-154411933-C-G, CADD 15.80
- Y31C (p.Tyr31Cys), rs2522920242, ClinGen CA415178529, ClinVar RCV002899360, Uncertain significance, 3-Methylglutaconic aciduria type 2
- Y31H (p.Tyr31His), gnomAD X-154411934-T-C, CADD 31.00, PolyPhen-2 0.99
- S32R (p.Ser32Arg), cosmic curated COSV50010
- C33G (p.Cys33Gly), gnomAD X-154411994-T-G, CADD 6.74
- C33C (p.Cys33Cys), rs1046778413, gnomAD X-154411996-C-T, CADD 10.70
- F34I (p.Phe34Ile), rs2522920277, ClinGen CA415178613, ClinVar RCV002646357, Uncertain significance, 3-Methylglutaconic aciduria type 2
- F34L (p.Phe34Leu), gnomAD rs1557190920
- F34F (p.Phe34Phe), gnomAD X-154411945-C-T, CADD 16.00
- T36A (p.Thr36Ala), cosmic curated COSV50010
- T36T (p.Thr36Thr), gnomAD X-154411951-C-A, CADD 15.30
- K37E (p.Lys37Glu), cosmic curated COSV50010
- K37K (p.Lys37Lys), rs2068326385, gnomAD X-154412087-G-A, CADD 18.40
- K37N (p.Lys37Asn), gnomAD X-154418595-G-T, CADD 7.61, SIFT 0.49
- Y38C (p.Tyr38Cys), rs2522923530, ClinGen CA415179311, ClinVar RCV002672147, CADD 16.30, PolyPhen-2 0.00, Uncertain significance, 3-Methylglutaconic aciduria type 2
- M39I (p.Met39Ile), rs1557191054, cosmic curated COSV99186, ClinGen CA415179341, ClinVar RCV002867055, AlphaMissense 0.66, MetaLR 0.91, Uncertain significance, 3-Methylglutaconic aciduria type 2
- M39V (p.Met39Val), gnomAD X-154412091-A-G, CADD 21.50, PolyPhen-2 0.14
- N40H (p.Asn40His), cosmic curated COSV99185, gnomAD rs1557191059, CADD 26.00, PolyPhen-2 0.73
- N40D (p.Asn40Asp), gnomAD X-154412094-A-G, CADD 24.30, PolyPhen-2 0.27
- H41L (p.His41Leu), NCI-TCGA Cosmic COSV5001, cosmic curated COSV50010, Variant assessed as somatic; moderate impact.
- H41N (p.His41Asn), gnomAD X-154412097-C-A, CADD 22.10, PolyPhen-2 0.18
- H41H (p.His41His), rs368329470, gnomAD X-154412099-C-T, CADD 11.10
- L42M (p.Leu42Met), TOPMed rs2068326989, gnomAD rs2068326989, CADD 24.70, PolyPhen-2 0.95, Uncertain significance, 3-Methylglutaconic aciduria type 2
- L42L (p.Leu42Leu), gnomAD X-154412102-G-T, CADD 10.40
- T43S (p.Thr43Ser), rs2522923680, ClinGen CA415179429, ClinVar RCV003054584, Uncertain significance, 3-Methylglutaconic aciduria type 2
- T43T (p.Thr43Thr), rs1451520068, gnomAD X-154412105-C-A, CADD 9.22
- V44M (p.Val44Met), gnomAD X-154412106-G-A, CADD 26.20, PolyPhen-2 0.95
- V44L (p.Val44Leu), gnomAD X-154412106-G-C, CADD 25.00, PolyPhen-2 0.64
- H45R (p.His45Arg), ExAC rs782760784, gnomAD rs782760784, CADD 24.90, PolyPhen-2 0.74
- H45H (p.His45His), gnomAD X-154412111-C-T, CADD 14.80
- N46Y (p.Asn46Tyr), rs2522923870, ClinGen CA415179495, ClinVar RCV003310695, Uncertain significance, Cardiovascular phenotype
- N46N (p.Asn46Asn), gnomAD X-154412114-C-T, CADD 15.10
- R47C (p.Arg47Cys), rs1429900386, gnomAD X-154418569-C-T, CADD 0.02, SIFT 0.12
- R47H (p.Arg47His), gnomAD X-154418570-G-A, CADD 0.17, SIFT 0.25
- E48K (p.Glu48Lys), rs2522923948, ClinGen CA415179536, ClinVar RCV002460457, Uncertain significance, Cardiovascular phenotype
- E48E (p.Glu48Glu), gnomAD X-154411972-G-A, CADD 15.40
- E48* (p.Glu48Ter), gnomAD X-154412118-G-T, CADD 37.00
- V49L (p.Val49Leu), rs2522924011, ClinGen CA415179573, ClinVar RCV002957525, Uncertain significance, 3-Methylglutaconic aciduria type 2
- V49M (p.Val49Met), gnomAD X-154412121-G-A, CADD 27.50, PolyPhen-2 1.00
- V49V (p.Val49Val), rs781869867, gnomAD X-154412123-G-A, CADD 14.30
- L50P (p.Leu50Pro), rs2522924071, ClinGen CA415179618, ClinVar RCV003237258, Uncertain significance, 3-Methylglutaconic aciduria type 2
- L50Q (p.Leu50Gln), rs2522924071, ClinGen CA415179615, ClinVar RCV002470525, Uncertain significance, 3-Methylglutaconic aciduria type 2
- Y51* (p.Tyr51Ter), rs104894941, ClinGen CA255717, ClinVar RCV000011850, ClinVar RCV001091834, Pathogenic
- Y51H (p.Tyr51His), gnomAD X-154412127-T-C, CADD 24.60, PolyPhen-2 1.00
- E52* (p.Glu52Ter), rs794729166, ClinGen CA308797, ClinVar RCV000183906, ClinVar RCV005089930, AlphaMissense 0.26, MetaLR 0.67, Pathogenic
- E52K (p.Glu52Lys), rs794729166, ClinGen CA415179650, NCI-TCGA Cosmic COSV5001, cosmic curated COSV50010, AlphaMissense 0.26, MetaLR 0.67, Uncertain significance, not provided; 3-Methylglutaconic aciduria type 2; Caused by mutation in the tafa
- E52Q (p.Glu52Gln), rs794729166, ClinGen CA415179654, ClinVar RCV003622338, ClinVar RCV005495629, AlphaMissense 0.26, MetaLR 0.67, Uncertain significance, 3-Methylglutaconic aciduria type 2; Cardiovascular phenotype
- E52E (p.Glu52Glu), gnomAD X-154412132-G-A, CADD 12.50
- I54M (p.Ile54Met), rs1557191093, ClinGen CA415179691, ClinVar RCV003821685, gnomAD rs1557191093, CADD 23.40, Uncertain significance, 3-Methylglutaconic aciduria type 2
- I54N (p.Ile54Asn), rs2522924321, ClinGen CA415179684, ClinVar RCV003237252, cosmic curated COSV99185, Uncertain significance, 3-Methylglutaconic aciduria type 2
- I54L (p.Ile54Leu), gnomAD X-154412136-A-C, CADD 23.90, PolyPhen-2 0.97
- I54F (p.Ile54Phe), gnomAD X-154412136-A-T, CADD 26.30, PolyPhen-2 1.00
- I54T (p.Ile54Thr), gnomAD X-154412137-T-C, CADD 28.00, PolyPhen-2 0.99
- E55* (p.Glu55Ter), rs2522924351, ClinGen CA415179696, ClinVar RCV003237272, CADD 36.00, Likely pathogenic
- K56E (p.Lys56Glu), TOPMed rs2068328473, CADD 22.60, PolyPhen-2 0.02, Uncertain significance, Cardiovascular phenotype
- K56Q (p.Lys56Gln), gnomAD X-154412142-A-C, CADD 22.50, PolyPhen-2 0.08
- R57L (p.Arg57Leu), UniProt VAR 084500, Pathogenic, in BTHS
- R57P (p.Arg57Pro), Ensembl rs2148186382
- R57Q (p.Arg57Gln), NCI-TCGA Cosmic COSV5001, cosmic curated COSV50010, Variant assessed as somatic; moderate impact., in BTHS
- G58S (p.Gly58Ser), cosmic curated COSV50011
- G58G (p.Gly58Gly), gnomAD X-154411987-G-A, CADD 7.50
- G58R (p.Gly58Arg), rs1468583691, gnomAD X-154412003-G-A, CADD 2.32
- G58E (p.Gly58Glu), gnomAD X-154412004-G-A, CADD 11.80
- P59Q (p.Pro59Gln), rs1557191098, NCI-TCGA Cosmic COSV9918, cosmic curated COSV99185, gnomAD rs1557191098, CADD 23.60, PolyPhen-2 0.95, Variant assessed as somatic; moderate impact.
- P59L (p.Pro59Leu), rs397515736, gnomAD X-154411980-C-T, CADD 6.78
- P59P (p.Pro59Pro), rs1557190940, gnomAD X-154411981-G-A, CADD 7.99
- P59S (p.Pro59Ser), gnomAD X-154411982-C-T, CADD 6.01
- P59H (p.Pro59His), rs1557190943, gnomAD X-154411983-C-A, CADD 6.20
- P59T (p.Pro59Thr), rs781904453, gnomAD X-154411991-C-A, CADD 4.98
- A60V (p.Ala60Val), rs2522924499, ClinGen CA415179795, ClinVar RCV002913648, CADD 21.60, PolyPhen-2 0.65, Uncertain significance, 3-Methylglutaconic aciduria type 2
- A60P (p.Ala60Pro), gnomAD X-154411965-AG-A, CADD 12.70
- A60S (p.Ala60Ser), gnomAD X-154411967-G-T, CADD 16.90
- A60T (p.Ala60Thr), rs781836148, gnomAD X-154411967-G-A, CADD 17.30
- A60D (p.Ala60Asp), gnomAD X-154411968-C-A, CADD 15.60
- A60A (p.Ala60Ala), gnomAD X-154412156-C-T, CADD 15.10
- T61M (p.Thr61Met), rs2522924558, ClinGen CA415179815, ClinVar RCV002727014, Uncertain significance, 3-Methylglutaconic aciduria type 2
- T61T (p.Thr61Thr), gnomAD X-154412159-G-A, CADD 6.95
- P62S (p.Pro62Ser), rs2068328744, ClinGen CA415179824, ClinVar RCV001306805, Ensembl rs2068328744, CADD 25.20, PolyPhen-2 1.00, Uncertain significance, 3-Methylglutaconic aciduria type 2
- P62P (p.Pro62Pro), rs1557191104, gnomAD X-154412162-C-G, CADD 11.10
- L63I (p.Leu63Ile), Ensembl rs868915029, CADD 25.20, PolyPhen-2 0.73
- L63L (p.Leu63Leu), rs1557191113, gnomAD X-154412165-C-T, CADD 15.90
- I64L (p.Ile64Leu), rs1322365208, ClinGen CA415179859, ClinVar RCV001338809, TOPMed rs1322365208, AlphaMissense 0.21, MetaLR 0.85, Uncertain significance, 3-Methylglutaconic aciduria type 2
- I64V (p.Ile64Val), TOPMed rs1322365208, gnomAD rs1322365208, AlphaMissense 0.21, MetaLR 0.85, Uncertain significance
- I64I (p.Ile64Ile), rs2148186482, gnomAD X-154412168-C-T, CADD 16.80
Public TAFAZZIN analysis runs
- TAFAZZIN analysis run — TAFAZZIN (479 variants) — completed 2026-08-19