RLBP1 (Retinaldehyde-binding protein 1) variants and mutations

RLBP1 (also known as Retinaldehyde-binding protein 1) is a human protein-coding gene encoding a retinaldehyde-binding protein 1 protein. It binds 11-cis-retinoids in retinal pigment epithelium and Muller cells and supports regeneration and trafficking of visual-cycle chromophore. Biallelic pathogenic variants cause retinal dystrophies including Bothnia dystrophy, retinitis punctata albescens, and fundus albipunctatus-like disease. This analysis covers 682 RLBP1 variants and mutations. Of these, 85% have computational variant effect predictions. Disease context includes Bothnia retinal dystrophy, fundus albipunctatus, and Newfoundland cone-rod dystrophy. Example RLBP1 variants include M1?, M1L, and S2*.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, MaveDB, LitVar.

Notable RLBP1 variants

Examples include M1?, M1L, S2*, S2L, S2T, E3D, E3K, E3Q. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.