PCSK1 (Neuroendocrine convertase 1) variants and mutations

PCSK1 (also known as Neuroendocrine convertase 1) is a human protein-coding gene encoding a neuroendocrine convertase 1 protein. It activates numerous peptide hormones and neuropeptides by cleaving their precursor proteins in endocrine and neuroendocrine secretory granules. Biallelic loss-of-function variants can cause severe early-onset obesity, endocrine abnormalities, and malabsorptive diarrhea. This analysis covers 1,097 PCSK1 variants and mutations. Of these, 95% have computational variant effect predictions. Disease context includes obesity due to prohormone convertase I deficiency, Abnormality of the skeletal system, and obesity disorder. Example PCSK1 variants include M1?, E2D, and E2K.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, MaveDB, LitVar.

Notable PCSK1 variants

Examples include M1?, E2D, E2K, R3L, R3Q, W6R, S7G, Q9H. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.