L104I (p.Leu104Ile) variant of NPC1 (O15118)

L104I (p.Leu104Ile) in NPC1 (O15118) is a missense change. Clinical records from ClinVar, EBI, and UniProt describe it as uncertain significance in the context of Niemann-Pick disease, type C1. The available variant effect predictions contribute to a CATVariant prioritization score of 0.53 / 1. The record also includes published literature and structural context.

L104I (p.Leu104Ile) variant details