FANCA (Fanconi anemia group A protein) variants and mutations

FANCA (also known as Fanconi anemia group A protein) is a human protein-coding gene encoding a fanconi anemia group A protein. It helps assemble the Fanconi-anemia core complex that monoubiquitinates FANCD2 and FANCI after DNA interstrand crosslinks stall replication. Biallelic loss-of-function variants are the most common cause of Fanconi anemia, with bone-marrow failure and cancer predisposition. This analysis covers 3,556 FANCA variants and mutations. Of these, 80% have computational variant effect predictions. Disease context includes Fanconi anemia complementation group A, Fanconi anemia, and acute myeloid leukemia. Example FANCA variants include M1?, M1C, and M1I.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.

Notable FANCA variants

Examples include M1?, M1C, M1I, M1L, M1R, M1T, M1V, S2A. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.