EP300 (Histone acetyltransferase p300) variants and mutations

EP300 (also known as Histone acetyltransferase p300) is a human protein-coding gene encoding a histone acetyltransferase p300 protein. It acetylates histones and transcription factors and acts as a central coactivator for developmental and stress-responsive transcription. Germline loss-of-function variants cause Rubinstein-Taybi syndrome type 2, while acquired alterations occur in several cancers. This analysis covers 6,833 EP300 variants and mutations. Of these, 39% have computational variant effect predictions. Disease context includes Rubinstein-Taybi syndrome due to EP300 haploinsufficiency, Menke-Hennekam syndrome 2, and cancer. Example EP300 variants include M1?, A2G, and A2V.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.

Notable EP300 variants

Examples include M1?, A2G, A2V, A2A, E3*, E3D, E3K, E3Q. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.