BEST1 (Bestrophin-1) variants and mutations

BEST1 (also known as Bestrophin-1) is a human protein-coding gene encoding a bestrophin-1 protein. It helps regulate ion transport and fluid homeostasis across the retinal pigment epithelium. Pathogenic variants cause bestrophinopathies including Best vitelliform macular dystrophy, autosomal recessive bestrophinopathy, and some retinitis pigmentosa phenotypes. This analysis covers 1,181 BEST1 variants and mutations. Of these, 80% have computational variant effect predictions. Disease context includes vitelliform macular dystrophy 2, autosomal recessive bestrophinopathy, and Best vitelliform macular dystrophy. Example BEST1 variants include M1V, T2S, and T2T.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, MaveDB, LitVar.

Notable BEST1 variants

Examples include M1V, T2S, T2T, I3N, I3T, I3V, T4I, T4N. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.