ACVRL1 (Activin receptor type-1-like) variants and mutations
ACVRL1 (also known as Activin receptor type-1-like) is a human protein-coding gene encoding an activin receptor type-1-like protein. It mediates BMP9 and BMP10 signaling in vascular endothelial cells and helps maintain normal vessel maturation and quiescence. Heterozygous loss-of-function variants cause hereditary hemorrhagic telangiectasia type 2, with telangiectasias and arteriovenous malformations. This analysis covers 1,141 ACVRL1 variants and mutations. Of these, 75% have computational variant effect predictions. Disease context includes hereditary hemorrhagic telangiectasia, telangiectasia, hereditary hemorrhagic, type 2, and pulmonary arterial hypertension. Example ACVRL1 variants include T2I, T2P, and T2T.
Variant analysis overview
- Gene: ACVRL1
- Protein: Activin receptor type-1-like
- UniProt accession: P37023
- Organism: Homo sapiens
- Variants analyzed: 1141
- Variant scope: all variants
- Completed: 2026-08-21
Variant and mutation evidence
- Variant composition: 846 unspecified-consequence records; 159 missense variants; 107 synonymous variants; 10 frameshift variants; 3 splice-region variants; 11 stop-gained variants; 2 in-frame deletions; 3 substitution
- Prediction scores: 861 variants have prediction scores (75% of the analyzed set).
Clinical, disease, and population context
- Disease context: 25 disease associations are represented. Top associations: hereditary hemorrhagic telangiectasia, telangiectasia, hereditary hemorrhagic, type 2, pulmonary arterial hypertension, vascular disorder, capillary disorder, Abnormality of the cardiovascular system, capillary malformation, pulmonary hypertension, primary, 1, heritable pulmonary arterial hypertension, epistaxis, hemophilia A, Telangiectasia.
Protein structure and variant hotspots
- Protein features: 1 transmembrane segments; 2 domains; 2 binding sites; 4 post-translational modification sites.
- Structural context: 649 variants have structural context.
- PTM context: 7 variants overlap post-translational modification sites.
Data sources
Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, ClinGen, MaveDB, LitVar.
Notable ACVRL1 variants
Examples include T2I, T2P, T2T, L3F, L3L, G4C, G4D, G4G. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.
- T2I (p.Thr2Ile), rs373062714, ClinGen CA6572777, ClinVar RCV001054999, ClinVar RCV005432552, REVEL 0.27, CADD 8.74, Uncertain significance, not provided; Telangiectasia, hereditary hemorrhagic, type 2
- T2P (p.Thr2Pro), gnomAD 12-51912442-A-C, CADD 0.42
- T2T (p.Thr2Thr), gnomAD 12-51912444-T-G, CADD 4.79
- L3F (p.Leu3Phe), ExAC rs779236098, TOPMed rs779236098, gnomAD rs779236098, CADD 7.44, Uncertain significance, not provided
- L3L (p.Leu3Leu), rs765849661, gnomAD 12-51912441-T-C, CADD 6.62
- G4C (p.Gly4Cys), NCI-TCGA TCGA novel, Variant assessed as somatic; moderate impact.
- G4D (p.Gly4Asp), NCI-TCGA Cosmic COSV6636, cosmic curated COSV66360, Variant assessed as somatic; moderate impact.
- G4G (p.Gly4Gly), gnomAD 12-51912486-C-A, CADD 5.48
- S5A (p.Ser5Ala), rs199658995, gnomAD 12-51912463-T-G, CADD 14.80
- S5P (p.Ser5Pro), gnomAD 12-51912463-T-C, CADD 12.90
- S5F (p.Ser5Phe), gnomAD 12-51912488-C-T, REVEL 0.39, CADD 0.40
- S5S (p.Ser5Ser), rs772291573, gnomAD 12-51912489-C-T, CADD 4.40
- P6R (p.Pro6Arg), gnomAD rs1485762988, REVEL 0.25, CADD 8.72
- P6S (p.Pro6Ser), rs759053428, gnomAD 12-51912445-C-T, CADD 1.41
- P6T (p.Pro6Thr), rs759053428, gnomAD 12-51912445-C-A, CADD 1.06
- P6L (p.Pro6Leu), rs1940711558, gnomAD 12-51912446-C-T, CADD 3.88
- P6P (p.Pro6Pro), rs778246850, gnomAD 12-51912492-C-T, CADD 4.73
- R7G (p.Arg7Gly), NCI-TCGA Cosmic COSV1011, cosmic curated COSV10118, REVEL 0.20, CADD 18.40, Variant assessed as somatic; moderate impact.
- R7K (p.Arg7Lys), gnomAD rs1940712916, REVEL 0.14, CADD 10.60
- K8E (p.Lys8Glu), Ensembl rs2139062670
- K8N (p.Lys8Asn), UniProt VAR 079583
- K8T (p.Lys8Thr), ExAC rs770506876, gnomAD rs770506876, REVEL 0.24, CADD 5.65
- K8K (p.Lys8Lys), rs776283937, gnomAD 12-51912498-A-G, CADD 6.17
- G9R (p.Gly9Arg), NCI-TCGA Cosmic COSV6636, cosmic curated COSV66360, Variant assessed as somatic; moderate impact.
- G9D (p.Gly9Asp), gnomAD 12-51912500-G-A, REVEL 0.25, CADD 2.82
- G9V (p.Gly9Val), gnomAD 12-51912500-G-T, REVEL 0.30, CADD 2.71
- G9G (p.Gly9Gly), gnomAD 12-51912501-C-A, CADD 2.66
- L10F (p.Leu10Phe), gnomAD 12-51912455-TGCTC, CADD 8.98
- L10S (p.Leu10Ser), rs764143924, gnomAD 12-51912456-GC-G, CADD 6.31
- L10H (p.Leu10His), gnomAD 12-51912458-T-A, CADD 12.80
- L10R (p.Leu10Arg), rs79549769, gnomAD 12-51912458-T-G, CADD 12.80
- L10P (p.Leu10Pro), gnomAD 12-51912458-T-C, CADD 12.50
- L11R (p.Leu11Arg), ExAC rs759002043, gnomAD rs759002043, REVEL 0.60, CADD 25.60
- M12I (p.Met12Ile), ExAC rs769326709, gnomAD rs769326709, REVEL 0.19, CADD 20.70
- M12T (p.Met12Thr), TOPMed rs1940713187, gnomAD rs1940713187, REVEL 0.27, CADD 21.50
- L13C (p.Leu13Cys), rs1085307404, ClinGen CA645293883, ClinVar RCV000488723, Pathogenic
- L13L (p.Leu13Leu), gnomAD 12-51912513-G-A, CADD 7.82
- L14L (p.Leu14Leu), rs1940713401, gnomAD 12-51912514-C-T, CADD 12.40
- M15T (p.Met15Thr), gnomAD 12-51912518-T-C, REVEL 0.21, CADD 20.90
- A16G (p.Ala16Gly), ExAC rs775260927, gnomAD rs775260927, REVEL 0.37, CADD 22.90
- A16V (p.Ala16Val), rs2277382, gnomAD 12-51912437-C-T, CADD 6.15
- A16T (p.Ala16Thr), gnomAD 12-51912466-G-A, CADD 3.98
- A16A (p.Ala16Ala), rs1409264215, gnomAD 12-51912522-C-G, CADD 12.10
- L17L (p.Leu17Leu), rs949831985, gnomAD 12-51912523-T-C, CADD 13.30
- V18M (p.Val18Met), cosmic curated COSV66361, ExAC rs762998725, gnomAD rs762998725, REVEL 0.31, CADD 19.20
- T19N (p.Thr19Asn), rs2540157150, ClinGen CA2582341783, ClinVar RCV003333622, Likely pathogenic
- T19S (p.Thr19Ser), gnomAD 12-51912472-A-T, CADD 18.10
- T19T (p.Thr19Thr), gnomAD 12-51912531-C-T, CADD 10.80
- Q20* (p.Gln20Ter), rs1555152345, ClinGen CA384896740, ClinVar RCV000640433, Ensembl rs1555152345, Pathogenic
- Q20R (p.Gln20Arg), gnomAD 12-51912529-AC-A, CADD 24.20
- Q20E (p.Gln20Glu), gnomAD 12-51912532-C-G, REVEL 0.21, CADD 6.38
- G21E (p.Gly21Glu), NCI-TCGA Cosmic COSV6636, cosmic curated COSV66360, Variant assessed as somatic; moderate impact.
- G21Y (p.Gly21Tyr), gnomAD 12-51912533-A-AGT, CADD 23.60
- G21V (p.Gly21Val), gnomAD 12-51913099-G-T, REVEL 0.35, CADD 26.90
- G21G (p.Gly21Gly), gnomAD 12-51913100-A-C, CADD 0.01
- D22A (p.Asp22Ala), Ensembl rs1592221445, Pathogenic
- D22H (p.Asp22His), NCI-TCGA Cosmic COSV1011, cosmic curated COSV10118, Variant assessed as somatic; moderate impact.
- D22Y (p.Asp22Tyr), gnomAD 12-51913101-G-T, REVEL 0.33, CADD 10.90
- D22E (p.Asp22Glu), gnomAD 12-51913103-C-A, REVEL 0.20, CADD 10.80
- D22D (p.Asp22Asp), gnomAD 12-51913103-C-T, CADD 5.88
- P23L (p.Pro23Leu), gnomAD rs1182091108
- P23S (p.Pro23Ser), gnomAD 12-51913104-C-T, REVEL 0.19, CADD 6.26
- P23A (p.Pro23Ala), gnomAD 12-51913104-C-G, REVEL 0.13, CADD 5.68
- P23H (p.Pro23His), gnomAD 12-51913105-C-A, REVEL 0.26, CADD 11.50
- P23P (p.Pro23Pro), gnomAD 12-51913106-T-A, CADD 0.22
- V24M (p.Val24Met), gnomAD 12-51913107-G-A, REVEL 0.26, CADD 2.64
- V24L (p.Val24Leu), gnomAD 12-51913107-G-T, REVEL 0.25, CADD 0.33
- V24V (p.Val24Val), gnomAD 12-51913109-G-T, CADD 7.38
- K25* (p.Lys25Ter), rs2540158136, ClinGen CA384897391, ClinVar RCV002380509, Pathogenic
- K25N (p.Lys25Asn), Ensembl rs1940728880, REVEL 0.21, CADD 16.30
- K25E (p.Lys25Glu), gnomAD 12-51913110-A-G, REVEL 0.24, CADD 16.00
- K25K (p.Lys25Lys), gnomAD 12-51913112-G-A, CADD 7.08
- P26L (p.Pro26Leu), rs199542304, ClinGen CA6572806, ClinVar RCV000865909, ClinVar RCV005540204, REVEL 0.31, CADD 17.40, Benign/Likely benign, Cardiovascular phenotype; Telangiectasia, hereditary hemorrhagic, type 2
- P26S (p.Pro26Ser), rs1442565422, gnomAD rs1442565422, REVEL 0.17, CADD 12.00, Variant assessed as somatic; moderate impact.
- P26T (p.Pro26Thr), gnomAD 12-51913113-C-A, REVEL 0.18, CADD 11.70
- P26A (p.Pro26Ala), gnomAD 12-51913113-C-G, REVEL 0.22, CADD 10.30
- P26Q (p.Pro26Gln), gnomAD 12-51913114-C-A, REVEL 0.29, CADD 16.90
- P26P (p.Pro26Pro), gnomAD 12-51913115-G-T, CADD 6.38
- S27F (p.Ser27Phe), gnomAD 12-51913117-C-T, REVEL 0.23, CADD 16.10
- S27Y (p.Ser27Tyr), gnomAD 12-51913117-C-A, REVEL 0.23, CADD 18.30
- S27S (p.Ser27Ser), gnomAD 12-51913118-T-C, CADD 7.55
- R28P (p.Arg28Pro), ExAC rs767447976, TOPMed rs767447976, gnomAD rs767447976, REVEL 0.46, CADD 12.90
- R28Q (p.Arg28Gln), ExAC rs767447976, TOPMed rs767447976, gnomAD rs767447976, REVEL 0.18, CADD 9.28
- R28W (p.Arg28Trp), rs761650726, ClinGen CA6572808, cosmic curated COSV10469, ClinVar RCV000994925, REVEL 0.37, CADD 16.90, Uncertain significance, Cardiovascular phenotype; not provided; Telangiectasia, hereditary hemorrhagic
- R28G (p.Arg28Gly), gnomAD 12-51913119-C-G, REVEL 0.22, CADD 12.30
- R28R (p.Arg28Arg), gnomAD 12-51913119-C-A, CADD 7.80
- R28L (p.Arg28Leu), gnomAD 12-51913120-G-T, REVEL 0.16, CADD 12.50
- G29D (p.Gly29Asp), Ensembl rs1486689063, REVEL 0.47, CADD 0.23
- G29S (p.Gly29Ser), gnomAD rs1940729566, REVEL 0.22, CADD 10.90
- G29C (p.Gly29Cys), gnomAD 12-51913122-G-T, REVEL 0.33, CADD 16.10
- G29V (p.Gly29Val), gnomAD 12-51913123-G-T, REVEL 0.33, CADD 0.64
- G29G (p.Gly29Gly), rs139486404, gnomAD 12-51913124-C-T, CADD 2.71
- P30L (p.Pro30Leu), rs765215717, cosmic curated COSV10532, ExAC rs765215717, gnomAD rs765215717, REVEL 0.19, CADD 9.85, Variant assessed as somatic; moderate impact.
- P30S (p.Pro30Ser), rs149664056, ClinGen CA211326, cosmic curated COSV66360, ClinVar RCV000148355, REVEL 0.50, CADD 10.60, Likely benign, Telangiectasia, hereditary hemorrhagic, type 2
- P30Q (p.Pro30Gln), gnomAD 12-51913126-C-A, REVEL 0.15, CADD 7.80
- P30P (p.Pro30Pro), rs373401329, gnomAD 12-51913127-G-A, CADD 5.75
- L31P (p.Leu31Pro), ExAC rs764616695, gnomAD rs764616695, REVEL 0.56, CADD 23.70
- L31L (p.Leu31Leu), gnomAD 12-51913130-G-A, CADD 10.90
- V32M (p.Val32Met), gnomAD rs1367771854
- T33I (p.Thr33Ile), TOPMed rs1940730238, REVEL 0.37, CADD 16.40
- T33N (p.Thr33Asn), gnomAD 12-51913135-C-A, REVEL 0.20, CADD 13.90
- T33T (p.Thr33Thr), gnomAD 12-51913136-C-A, CADD 10.80
- C34* (p.Cys34Ter), rs1226848374, ClinGen CA384897514, ClinVar RCV001221492, ClinVar RCV002379838, CADD 33.00, Pathogenic, in HHT2
- C34R (p.Cys34Arg), rs2540158250, ClinGen CA384897505, ClinVar RCV002583485, REVEL 0.94, CADD 26.80, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C34S (p.Cys34Ser), rs2540158250, ClinGen CA384897503, ClinVar RCV003842958, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C34W (p.Cys34Trp), TOPMed rs1226848374, gnomAD rs1226848374, Pathogenic, in HHT2
- C34Y (p.Cys34Tyr), rs2540158265, ClinGen CA384897509, ClinVar RCV002378063, ClinVar RCV003098413, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2; Cardiovascular phenotype
- C34F (p.Cys34Phe), gnomAD 12-51913138-G-T, REVEL 0.92, CADD 26.50
- C34C (p.Cys34Cys), rs1226848374, gnomAD 12-51913139-C-T, CADD 8.52
- T35K (p.Thr35Lys), NCI-TCGA Cosmic COSV6635, cosmic curated COSV66359, REVEL 0.44, CADD 16.20, Variant assessed as somatic; moderate impact.
- T35M (p.Thr35Met), rs376537508, ClinGen CA6572815, ClinVar RCV002401089, ClinVar RCV005008573, REVEL 0.31, CADD 11.80, Uncertain significance, Cardiovascular phenotype; Telangiectasia, hereditary hemorrhagic, type 2
- T35A (p.Thr35Ala), gnomAD 12-51913140-A-G, REVEL 0.23, CADD 14.50
- T35T (p.Thr35Thr), rs757588086, gnomAD 12-51913142-G-C, CADD 0.19
- C36R (p.Cys36Arg), rs2139064443, ClinGen CA384897534, ClinVar RCV001378120, Ensembl rs2139064443, AlphaMissense 0.95, MetaLR 0.95, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C36Y (p.Cys36Tyr), rs2540158303, ClinGen CA384897542, ClinVar RCV002424385, REVEL 0.88, CADD 24.70, Likely pathogenic, Cardiovascular phenotype
- C36F (p.Cys36Phe), gnomAD 12-51913144-G-T, REVEL 0.89, CADD 24.50
- E37D (p.Glu37Asp), ExAC rs781586192, TOPMed rs781586192, gnomAD rs781586192, REVEL 0.26, CADD 2.68, Likely benign
- E37Q (p.Glu37Gln), NCI-TCGA TCGA novel, Variant assessed as somatic; moderate impact.
- E37E (p.Glu37Glu), rs781586192, gnomAD 12-51913148-G-A, CADD 2.18
- S38C (p.Ser38Cys), rs2540158317, ClinGen CA384897561, ClinVar RCV002320469, UniProt VAR 070310, Uncertain significance, Cardiovascular phenotype
- S38N (p.Ser38Asn), rs1257219446, ClinGen CA384897562, ClinVar RCV002667875, TOPMed rs1257219446, REVEL 0.32, CADD 0.00, Uncertain significance, Telangiectasia, hereditary hemorrhagic, type 2
- S38I (p.Ser38Ile), gnomAD 12-51913150-G-T, REVEL 0.35, CADD 0.01
- S38R (p.Ser38Arg), gnomAD 12-51913151-C-A, REVEL 0.32, CADD 8.51
- S38S (p.Ser38Ser), gnomAD 12-51913151-C-T, CADD 6.33
- P39L (p.Pro39Leu), gnomAD rs1202637291
- P39T (p.Pro39Thr), gnomAD rs1459735315, REVEL 0.25, CADD 9.52
- P39S (p.Pro39Ser), gnomAD 12-51913152-C-T, REVEL 0.24, CADD 9.39
- P39R (p.Pro39Arg), gnomAD 12-51913153-C-G, REVEL 0.36, CADD 11.60
- H40L (p.His40Leu), gnomAD rs1248476778, REVEL 0.27, CADD 9.10
- H40Y (p.His40Tyr), gnomAD 12-51913155-C-T, REVEL 0.27, CADD 4.76
- H40H (p.His40His), rs745507845, gnomAD 12-51913157-T-C, CADD 4.11
- C41G (p.Cys41Gly), rs2139064528, ClinGen CA384897602, ClinVar RCV001382876, Ensembl rs2139064528, AlphaMissense 0.86, MetaLR 0.91, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C41Y (p.Cys41Tyr), rs1184716348, ClinGen CA384897604, ClinVar RCV001065552, UniProt VAR 075232, AlphaMissense 0.97, MetaLR 0.96, Likely pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C41F (p.Cys41Phe), gnomAD 12-51913159-G-T, REVEL 0.88, CADD 26.30
- C41* (p.Cys41Ter), gnomAD 12-51913160-C-A, CADD 36.00
- K42N (p.Lys42Asn), NCI-TCGA TCGA novel, REVEL 0.19, CADD 14.30, Variant assessed as somatic; high impact.
- K42Q (p.Lys42Gln), gnomAD rs1418659982, REVEL 0.27, CADD 15.40
- K42M (p.Lys42Met), gnomAD 12-51913162-A-T, REVEL 0.46, CADD 11.40
- K42K (p.Lys42Lys), gnomAD 12-51913163-G-A, CADD 8.64
- G43D (p.Gly43Asp), rs2540158393, ClinGen CA2580086429, ClinVar RCV002376523, Pathogenic
- G43R (p.Gly43Arg), 1000Genomes rs199652672, ExAC rs199652672, TOPMed rs199652672, gnomAD rs199652672, REVEL 0.36, CADD 15.10, Uncertain significance, Telangiectasia, hereditary hemorrhagic, type 2
- G43V (p.Gly43Val), gnomAD rs1940731581, REVEL 0.36, CADD 16.70
- G43W (p.Gly43Trp), gnomAD 12-51913164-G-T, REVEL 0.50, CADD 23.20
- G43G (p.Gly43Gly), gnomAD 12-51913166-G-T, CADD 6.76
- P44C (p.Pro44Cys), rs2540158399, ClinGen CA2580086430, ClinVar RCV002380826, Pathogenic
- P44L (p.Pro44Leu), TOPMed rs1940731729, gnomAD rs1940731729, REVEL 0.34, CADD 16.60
- P44S (p.Pro44Ser), ExAC rs779576094, gnomAD rs779576094, REVEL 0.22, CADD 7.03
- P44T (p.Pro44Thr), gnomAD 12-51913167-C-A, REVEL 0.21, CADD 6.85
- P44H (p.Pro44His), gnomAD 12-51913168-C-A, REVEL 0.40, CADD 16.30
- P44P (p.Pro44Pro), gnomAD 12-51913169-T-C, CADD 4.12
- T45I (p.Thr45Ile), ExAC rs748772777, gnomAD rs748772777, REVEL 0.24, CADD 16.20
- T45N (p.Thr45Asn), NCI-TCGA Cosmic COSV6635, cosmic curated COSV66359, Variant assessed as somatic; moderate impact.
- C46G (p.Cys46Gly), UniProt VAR 075233, Pathogenic, in HHT2
- C46S (p.Cys46Ser), rs1555152454, ClinGen CA384897664, ClinVar RCV000640437, ClinVar RCV003303025, AlphaMissense 0.98, MetaLR 1.00, Likely pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C46F (p.Cys46Phe), gnomAD 12-51913174-G-T, REVEL 0.88, CADD 26.30
- R47G (p.Arg47Gly), ExAC rs768072967, TOPMed rs768072967, gnomAD rs768072967, Likely pathogenic, in HHT2
- R47L (p.Arg47Leu), ExAC rs774389618, TOPMed rs774389618, gnomAD rs774389618, REVEL 0.35, CADD 9.51, Pathogenic, in HHT2
- R47P (p.Arg47Pro), rs774389618, ClinGen CA16607361, ClinVar RCV000426666, ClinVar RCV002272232, REVEL 0.59, CADD 13.40, Pathogenic/Likely pathogenic, Cardiovascular phenotype; Telangiectasia, hereditary hemorrhagic, type 2; not pr
- R47Q (p.Arg47Gln), rs774389618, ClinGen CA6572823, NCI-TCGA Cosmic COSV6635, cosmic curated COSV66359, REVEL 0.30, CADD 6.34, Uncertain significance, not provided
- R47W (p.Arg47Trp), rs768072967, ClinGen CA6572822, NCI-TCGA Cosmic COSV6636, cosmic curated COSV66360, REVEL 0.40, CADD 22.60, Uncertain significance, Telangiectasia, hereditary hemorrhagic, type 2
- R47R (p.Arg47Arg), gnomAD 12-51913176-C-A, CADD 12.70
- G48E (p.Gly48Glu), rs267606632, ClinGen CA270765, ClinVar RCV000144434, ClinVar RCV002390302, AlphaMissense 0.77, MetaLR 0.92, Pathogenic/Likely pathogenic, Cardiovascular phenotype; Telangiectasia, hereditary hemorrhagic, type 2
- G48R (p.Gly48Arg), rs2139064757, ClinGen CA384897677, ClinVar RCV001897578, Ensembl rs2139064757, AlphaMissense 0.90, MetaLR 0.94, Pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- G48V (p.Gly48Val), gnomAD 12-51913180-G-T, REVEL 0.74, CADD 25.20
- G48G (p.Gly48Gly), gnomAD 12-51913181-G-T, CADD 7.62
- A49G (p.Ala49Gly), cosmic curated COSV66360, TOPMed rs1169329926, gnomAD rs1169329926, REVEL 0.30, CADD 13.00
- A49P (p.Ala49Pro), rs863223415, NCI-TCGA Cosmic COSV6635, not provided, Telangiectasia, hereditary hemorrhagic, type 2
- A49T (p.Ala49Thr), ExAC rs267606633, TOPMed rs267606633, gnomAD rs267606633, REVEL 0.35, CADD 7.64
- A49V (p.Ala49Val), cosmic curated COSV66359, TOPMed rs1169329926, gnomAD rs1169329926, REVEL 0.23, CADD 13.00, Uncertain significance, not specified
- A49S (p.Ala49Ser), gnomAD 12-51913182-G-T, REVEL 0.32, CADD 4.88
- A49D (p.Ala49Asp), gnomAD 12-51913183-C-A, REVEL 0.33, CADD 11.20
- W50C (p.Trp50Cys), rs121909285, ClinGen CA384897711, ClinVar RCV001959004, UniProt VAR 006204, REVEL 0.64, CADD 25.60, Pathogenic, Cardiovascular phenotype; not provided; Telangiectasia, hereditary hemorrhagic
- W50G (p.Trp50Gly), rs1555152468, ClinGen CA384897704, ClinVar RCV002017836, Ensembl rs1555152468, AlphaMissense 0.72, MetaLR 0.64, Likely pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- W50L (p.Trp50Leu), Ensembl rs867439593, REVEL 0.49, CADD 21.40
- W50R (p.Trp50Arg), rs1555152468, ClinGen CA384897700, ClinVar RCV000558413, ClinVar RCV002512113, REVEL 0.54, AlphaMissense 0.72, Likely pathogenic, Hereditary hemorrhagic telangiectasia; Telangiectasia, hereditary hemorrhagic, t
- W50* (p.Trp50Ter), gnomAD 12-51913186-G-A, CADD 36.00
- C51G (p.Cys51Gly), rs2139064874, ClinGen CA384897717, ClinVar RCV001895308, ClinVar RCV002388756, AlphaMissense 0.91, MetaLR 0.99, Likely pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C51S (p.Cys51Ser), rs2139064874, ClinGen CA384897713, ClinVar RCV003036774, AlphaMissense 0.91, MetaLR 0.99, Likely pathogenic, Telangiectasia, hereditary hemorrhagic, type 2
- C51Y (p.Cys51Tyr), rs863223409, ClinGen CA324720, ClinVar RCV000200161, ClinVar RCV001857712, AlphaMissense 0.97, MetaLR 0.99, Pathogenic, not provided; Cardiovascular phenotype; Telangiectasia, hereditary hemorrhagic
- C51F (p.Cys51Phe), gnomAD 12-51913189-G-T, REVEL 0.91, CADD 26.70
Public ACVRL1 analysis runs
- ACVRL1 analysis run — ACVRL1 (1,141 variants) — completed 2026-08-21