ABCA3 (Q99758) variants and mutations

ABCA3 (also known as Q99758) is a human protein-coding gene encoding a phospholipid-transporting ATPase protein. It transports phospholipids into lamellar bodies of alveolar type II cells, supporting pulmonary surfactant assembly and normal gas exchange. Biallelic loss-of-function variants can cause neonatal respiratory failure or childhood interstitial lung disease. This analysis covers 2,358 ABCA3 variants and mutations. Of these, 86% have computational variant effect predictions. Disease context includes Neonatal acute respiratory distress with surfactant metabolism deficiency, Congenital pulmonary alveolar proteinosis, and hereditary pulmonary alveolar proteinosis. Example ABCA3 variants include A2D, A2T, and A2V.

Variant analysis overview

Variant and mutation evidence

Clinical, disease, and population context

Protein structure and variant hotspots

Data sources

Evidence in this analysis draws on EBI Proteins Variation, UniProt, gnomAD v4, EuropePMC, 3D Hotspot Analysis, Interaction Network Analysis, Protein Data Bank, AlphaFold DB, gnomAD constraint, Open Targets, MaveDB, LitVar.

Notable ABCA3 variants

Examples include A2D, A2T, A2V, V3A, V3M, L4F, R5T, Q6R. Listed records include available protein-change notation, database identifiers, clinical classifications, computational predictions, population evidence, experimental measurements, and disease context.