Parkinsonism-dystonia, infantile: genes and variants

Parkinsonism-dystonia, infantile is linked to 1 analyzed protein (SLC6A3). 1 DNA variants are known to cause it; 109 more are uncertain, and 0 of those already look disease-causing on computable evidence.

Last updated 2026-09-30. Research information, not medical advice.

Genes linked to Parkinsonism-dystonia, infantile

Known disease-causing variants in Parkinsonism-dystonia, infantile

VariantPositionProtein partClinical label
SLC6A3 G386R386ExtracellularDisease-causing (★)

Same protein, different disease

Diseases related to Parkinsonism-dystonia, infantile

Frequently asked questions

Which genes are linked to Parkinsonism-dystonia, infantile?

In CATVariant, Parkinsonism-dystonia, infantile is linked to 1 analyzed protein: SLC6A3 (Sodium-dependent dopamine transporter).

How many genetic variants are linked to Parkinsonism-dystonia, infantile?

115 variants: 1 are classified as disease-causing (pathogenic or likely pathogenic) in ClinVar and 109 are of uncertain significance or have conflicting reports.

Which uncertain variants in Parkinsonism-dystonia, infantile look disease-causing?

None of the uncertain variants currently reaches the likely-pathogenic range on computable evidence alone.

About this data

Variant–disease links come from ClinVar, Open Targets and UniProt, pooled from the latest public CATVariant analysis of each human protein. Evidence scores use the ACMG/AMP Bayesian points scale with computable criteria only (position among known disease variants, rarity in gnomAD, calibrated predictors, deep mutational scanning); there is no family or patient data, so they prioritise variants for expert review and never classify them.

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