Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency: genes and variants

Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency is linked to 1 analyzed protein (MMUT). 53 DNA variants are known to cause it; 10 more are uncertain, and 1 of those already look disease-causing on computable evidence.

Last updated 2026-09-30. Research information, not medical advice.

Genes linked to Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency

Known disease-causing variants in Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency

VariantPositionProtein partClinical label
MMUT G94R94Disease-causing (★★)
MMUT G215S215Disease-causing (★★)
MMUT G215C215Disease-causing (★★)
MMUT R326K326Disease-causing (★★)
MMUT R326G326Disease-causing (★★)
MMUT R93H93Disease-causing (★★)
MMUT R93C93Disease-causing (★★)
MMUT G94V94Disease-causing (★★)
MMUT R108H108Disease-causing (★★)
MMUT R108C108Disease-causing (★★)
MMUT R369C369Disease-causing (★★)
MMUT R369H369Disease-causing (★★)
MMUT W105R105Disease-causing (★★)
MMUT A141E141Disease-causing (★★)
MMUT G145S145Disease-causing (★★)
MMUT T230R230Disease-causing (★★)
MMUT L305S305Disease-causing (★★)
MMUT A324T324Disease-causing (★★)
MMUT L358P358Disease-causing (★★)
MMUT T387P387Disease-causing (★★)
MMUT R616C616B12-bindingDisease-causing (★★)
MMUT G670R670B12-bindingDisease-causing (★★)
MMUT P86L86Disease-causing (★★)
MMUT A191E191Disease-causing (★★)
MMUT Q218H218Disease-causing (★★)
MMUT N219Y219Disease-causing (★★)
MMUT Y316C316Disease-causing (★★)
MMUT L328P328Disease-causing (★★)
MMUT T370P370Disease-causing (★★)
MMUT A377E377Disease-causing (★★)
MMUT R403Q403Disease-causing (★★)
MMUT G426R426Disease-causing (★★)
MMUT G427D427Disease-causing (★★)
MMUT Y429C429Disease-causing (★★)
MMUT G623R623B12-bindingDisease-causing (★★)
MMUT H627R627B12-bindingDisease-causing (★★)
MMUT G630E630B12-bindingDisease-causing (★★)
MMUT G642R642B12-bindingDisease-causing (★★)
MMUT G717V717B12-bindingDisease-causing (★★)
MMUT Y110C110Disease-causing (★★)
MMUT G203R203Disease-causing (★★)
MMUT L674F674B12-bindingDisease-causing (★★)
MMUT A555T555Disease-causing (★★)
MMUT A676T676B12-bindingDisease-causing (★★)
MMUT R694W694B12-bindingDisease-causing (★★)
MMUT M1T1Disease-causing (★★)
MMUT V136F136Disease-causing (★★)
MMUT Q109R109Disease-causing (★)
MMUT H143Y143Disease-causing (★)
MMUT G161R161Disease-causing (★)
MMUT F337L337Disease-causing (★)
MMUT G87E87Disease-causing (★)
MMUT G454E454Disease-causing (★)

Uncertain variants in Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency that look disease-causing

VariantPositionProtein partClinical labelEvidence
MMUT A141V141Conflicting reports (★)+6: 2 other pathogenic changes within 3 positions; A141E at the same position is pathogenic; REVEL 0.866

Same protein, different disease

Diseases related to Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency

Frequently asked questions

Which genes are linked to Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency?

In CATVariant, Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency is linked to 1 analyzed protein: MMUT (Methylmalonyl-CoA mutase, mitochondrial).

How many genetic variants are linked to Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency?

63 variants: 53 are classified as disease-causing (pathogenic or likely pathogenic) in ClinVar and 10 are of uncertain significance or have conflicting reports.

Which uncertain variants in Methylmalonic aciduria due to complete methylmalonyl-CoA mutase deficiency look disease-causing?

1 uncertain variants reach the likely-pathogenic range of the ACMG/AMP points scale on computable evidence, for example MMUT A141V. These are leads for expert review, not diagnoses.

About this data

Variant–disease links come from ClinVar, Open Targets and UniProt, pooled from the latest public CATVariant analysis of each human protein. Evidence scores use the ACMG/AMP Bayesian points scale with computable criteria only (position among known disease variants, rarity in gnomAD, calibrated predictors, deep mutational scanning); there is no family or patient data, so they prioritise variants for expert review and never classify them.

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