Glutaric acidemia IIc: genes and variants

Glutaric acidemia IIc is linked to 1 analyzed protein (ETFDH). 51 DNA variants are known to cause it; 17 more are uncertain, and 2 of those already look disease-causing on computable evidence.

Last updated 2026-09-30. Research information, not medical advice.

Also known as: Glutaric acidemia type 2C

Genes linked to Glutaric acidemia IIc

Weakly linked (only a few uncertain records): ETFB.

Where Glutaric acidemia IIc variants cluster

Known disease-causing variants in Glutaric acidemia IIc

VariantPositionProtein partClinical label
ETFDH L127H127Disease-causing (★★)
ETFDH L127P127Disease-causing (★★)
ETFDH R175L175Disease-causing (★★)
ETFDH R175H175Disease-causing (★★)
ETFDH G611R611Disease-causing (★★)
ETFDH R175C175Disease-causing (★★)
ETFDH G611E611Disease-causing (★★)
ETFDH S82P82Disease-causing (★★)
ETFDH R358K358Disease-causing (★★)
ETFDH Y361C361Disease-causing (★★)
ETFDH M404T404Disease-causing (★★)
ETFDH G467R467IntramembraneDisease-causing (★★)
ETFDH H529R529Disease-causing (★★)
ETFDH D130V130Disease-causing (★★)
ETFDH L138R138Disease-causing (★★)
ETFDH L334P334Disease-causing (★★)
ETFDH P456S456Disease-causing (★★)
ETFDH P456L456Disease-causing (★★)
ETFDH G472R472IntramembraneDisease-causing (★★)
ETFDH P483L483IntramembraneDisease-causing (★★)
ETFDH W484R484IntramembraneDisease-causing (★★)
ETFDH G610R610Disease-causing (★★)
ETFDH M1I1Disease-causing (★★)
ETFDH M1T1Disease-causing (★★)
ETFDH V174A174Disease-causing (★★)
ETFDH L176F176Disease-causing (★★)
ETFDH P227T227Disease-causing (★★)
ETFDH Y333C333Disease-causing (★★)
ETFDH G356E356Disease-causing (★★)
ETFDH L377P377Disease-causing (★★)
ETFDH L409F409Disease-causing (★★)
ETFDH T485S485Disease-causing (★★)
ETFDH S35P35Disease-causing (★★)
ETFDH R99C99Disease-causing (★★)
ETFDH R155G155IntramembraneDisease-causing (★★)
ETFDH A215T215Disease-causing (★★)
ETFDH Y257C257Disease-causing (★★)
ETFDH G272R272Disease-causing (★★)
ETFDH G362R362Disease-causing (★★)
ETFDH V451L451Disease-causing (★★)
ETFDH Y553H553Disease-causing (★★)
ETFDH E557K557Disease-causing (★★)
ETFDH E567K567Disease-causing (★★)
ETFDH E185K185Disease-causing (★★)
ETFDH Q222P222Disease-causing (★★)
ETFDH E246K246Disease-causing (★★)
ETFDH V291G291Disease-causing (★★)
ETFDH S307C307Disease-causing (★★)
ETFDH P27S27Disease-causing (★★)
ETFDH E193K193Disease-causing (★)
ETFDH A84T84Disease-causing

Uncertain variants in Glutaric acidemia IIc that look disease-causing

VariantPositionProtein partClinical labelEvidence
ETFDH P227S227Conflicting reports (★)+7: in a 3D region that tolerates change poorly (1R); P227T at the same position is pathogenic; seen in 6.6e-06 of gnomAD DNA copies; REVEL 0.782
ETFDH G610A610Uncertain+6: 3 other pathogenic changes within 3 positions; G610R at the same position is pathogenic; seen in 6.8e-07 of gnomAD DNA copies; REVEL 0.704

Which prediction tools work for Glutaric acidemia IIc

How often each tool ranks a disease-causing variant above a harmless one (AUROC × 100).

Same protein, different disease

Diseases related to Glutaric acidemia IIc

Frequently asked questions

Which genes are linked to Glutaric acidemia IIc?

In CATVariant, Glutaric acidemia IIc is linked to 1 analyzed protein: ETFDH (Electron transfer flavoprotein-ubiquinone oxidoreductase, mitochondrial).

How many genetic variants are linked to Glutaric acidemia IIc?

71 variants: 51 are classified as disease-causing (pathogenic or likely pathogenic) in ClinVar and 17 are of uncertain significance or have conflicting reports.

Which uncertain variants in Glutaric acidemia IIc look disease-causing?

2 uncertain variants reach the likely-pathogenic range of the ACMG/AMP points scale on computable evidence, for example ETFDH P227S and ETFDH G610A. These are leads for expert review, not diagnoses.

Which variant effect predictor works best for Glutaric acidemia IIc?

Among tools not trained on clinical labels, SIFT separates this disease's known disease-causing variants from harmless ones best (AUROC 0.98, based on 44 disease-causing and 8 harmless variants).

About this data

Variant–disease links come from ClinVar, Open Targets and UniProt, pooled from the latest public CATVariant analysis of each human protein. Evidence scores use the ACMG/AMP Bayesian points scale with computable criteria only (position among known disease variants, rarity in gnomAD, calibrated predictors, deep mutational scanning); there is no family or patient data, so they prioritise variants for expert review and never classify them.

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