Childhood hypophosphatasia: genes and variants

Childhood hypophosphatasia is linked to 1 analyzed protein (ALPL). 60 DNA variants are known to cause it; 48 more are uncertain, and 1 of those already look disease-causing on computable evidence.

Last updated 2026-09-30. Research information, not medical advice.

Genes linked to Childhood hypophosphatasia

Known disease-causing variants in Childhood hypophosphatasia

VariantPositionProtein partClinical label
ALPL A443V443Disease-causing (★★★★)
ALPL A443S443Disease-causing (★★★★)
ALPL A176T176Disease-causing (★★★★)
ALPL G220E220Disease-causing (★★)
ALPL G220A220Disease-causing (★★)
ALPL E476A476Disease-causing (★★)
ALPL A468V468Disease-causing (★★)
ALPL E476K476Disease-causing (★★)
ALPL G63V63Disease-causing (★★)
ALPL R71H71Disease-causing (★★)
ALPL I72T72Disease-causing (★★)
ALPL T167M167Disease-causing (★★)
ALPL Y178H178Disease-causing (★★)
ALPL A179T179Disease-causing (★★)
ALPL R184Q184Disease-causing (★★)
ALPL M226I226Disease-causing (★★)
ALPL G334D334Disease-causing (★★)
ALPL D337G337Disease-causing (★★)
ALPL A377V377Disease-causing (★★)
ALPL D378V378Disease-causing (★★)
ALPL S445P445Disease-causing (★★)
ALPL E452K452Disease-causing (★★)
ALPL G473S473Disease-causing (★★)
ALPL T100M100Disease-causing (★★)
ALPL A132G132Disease-causing (★★)
ALPL A132V132Disease-causing (★★)
ALPL R272C272Disease-causing (★★)
ALPL R272H272Disease-causing (★★)
ALPL E311K311Disease-causing (★★)
ALPL F327L327Disease-causing (★★)
ALPL H381R381Disease-causing (★★)
ALPL R391C391Disease-causing (★★)
ALPL A468S468Disease-causing (★★)
ALPL A123D123Disease-causing (★★)
ALPL T134H134Disease-causing (★★)
ALPL M219I219Disease-causing (★★)
ALPL R246S246Disease-causing (★★)
ALPL D306Y306Disease-causing (★★)
ALPL H341R341Disease-causing (★★)
ALPL G426S426Disease-causing (★★)
ALPL H472R472Disease-causing (★★)
ALPL A487V487Disease-causing (★★)
ALPL E298K298Disease-causing (★★)
ALPL A348T348Disease-causing (★★)
ALPL V374M374Disease-causing (★★)
ALPL V382I382Disease-causing (★★)
ALPL Y388C388Disease-causing (★★)
ALPL I395V395Disease-causing (★★)
ALPL G455S455Disease-causing (★★)
ALPL G491R491Disease-causing (★★)
ALPL N493K493Disease-causing (★★)
ALPL M1V1Disease-causing (★★)
ALPL I359M359Disease-causing (★★)
ALPL T411A411Disease-causing (★★)
ALPL K264R264Disease-causing (★★)
ALPL G221A221Disease-causing (★)
ALPL A33V33Disease-causing (★)
ALPL G129E129Disease-causing (★)
ALPL M295L295Disease-causing (★)
ALPL G144A144Disease-causing (★)

Uncertain variants in Childhood hypophosphatasia that look disease-causing

VariantPositionProtein partClinical labelEvidence
ALPL E452G452Uncertain (★)+7: 2 other pathogenic changes within 3 positions; E452K at the same position is pathogenic; seen in 6.6e-06 of gnomAD DNA copies; REVEL 0.848

Same protein, different disease

Diseases related to Childhood hypophosphatasia

Frequently asked questions

Which genes are linked to Childhood hypophosphatasia?

In CATVariant, Childhood hypophosphatasia is linked to 1 analyzed protein: ALPL (Alkaline phosphatase, tissue-nonspecific isozyme).

How many genetic variants are linked to Childhood hypophosphatasia?

109 variants: 60 are classified as disease-causing (pathogenic or likely pathogenic) in ClinVar and 48 are of uncertain significance or have conflicting reports.

Which uncertain variants in Childhood hypophosphatasia look disease-causing?

1 uncertain variants reach the likely-pathogenic range of the ACMG/AMP points scale on computable evidence, for example ALPL E452G. These are leads for expert review, not diagnoses.

About this data

Variant–disease links come from ClinVar, Open Targets and UniProt, pooled from the latest public CATVariant analysis of each human protein. Evidence scores use the ACMG/AMP Bayesian points scale with computable criteria only (position among known disease variants, rarity in gnomAD, calibrated predictors, deep mutational scanning); there is no family or patient data, so they prioritise variants for expert review and never classify them.

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