Autosomal recessive ataxia due to ubiquinone deficiency: genes and variants

Autosomal recessive ataxia due to ubiquinone deficiency is linked to 1 analyzed protein (COQ8A). 23 DNA variants are known to cause it; 37 more are uncertain, and 0 of those already look disease-causing on computable evidence.

Last updated 2026-09-30. Research information, not medical advice.

Genes linked to Autosomal recessive ataxia due to ubiquinone deficiency

Where Autosomal recessive ataxia due to ubiquinone deficiency variants cluster

Known disease-causing variants in Autosomal recessive ataxia due to ubiquinone deficiency

VariantPositionProtein partClinical label
COQ8A R301Q301Disease-causing (★★)
COQ8A A304T304Disease-causing (★★)
COQ8A A304V304Disease-causing (★★)
COQ8A L277P277KxGQ motifDisease-causing (★★)
COQ8A R299W299Disease-causing (★★)
COQ8A R301W301Disease-causing (★★)
COQ8A A338T338Protein kinaseDisease-causing (★★)
COQ8A A338V338Protein kinaseDisease-causing (★★)
COQ8A R213Q213Disease-causing (★★)
COQ8A R213W213Disease-causing (★★)
COQ8A M555I555Disease-causing (★★)
COQ8A T511M511Protein kinaseDisease-causing (★★)
COQ8A G272C272Disease-causing (★)
COQ8A G272A272Disease-causing (★)
COQ8A K276R276KxGQ motifDisease-causing (★)
COQ8A Q279P279KxGQ motifDisease-causing (★)
COQ8A G615D615Disease-causing (★)
COQ8A L459P459Protein kinaseDisease-causing (★)
COQ8A G272D272Disease-causing
COQ8A R271C271Disease-causing
COQ8A P207L207Disease-causing
COQ8A Y514C514Protein kinaseDisease-causing
COQ8A E551K551Disease-causing

Which prediction tools work for Autosomal recessive ataxia due to ubiquinone deficiency

How often each tool ranks a disease-causing variant above a harmless one (AUROC × 100).

Diseases related to Autosomal recessive ataxia due to ubiquinone deficiency

Frequently asked questions

Which genes are linked to Autosomal recessive ataxia due to ubiquinone deficiency?

In CATVariant, Autosomal recessive ataxia due to ubiquinone deficiency is linked to 1 analyzed protein: COQ8A (Atypical kinase COQ8A, mitochondrial).

How many genetic variants are linked to Autosomal recessive ataxia due to ubiquinone deficiency?

87 variants: 23 are classified as disease-causing (pathogenic or likely pathogenic) in ClinVar and 37 are of uncertain significance or have conflicting reports.

Which uncertain variants in Autosomal recessive ataxia due to ubiquinone deficiency look disease-causing?

None of the uncertain variants currently reaches the likely-pathogenic range on computable evidence alone.

Which variant effect predictor works best for Autosomal recessive ataxia due to ubiquinone deficiency?

Among tools not trained on clinical labels, SIFT separates this disease's known disease-causing variants from harmless ones best (AUROC 0.95, based on 21 disease-causing and 11 harmless variants).

About this data

Variant–disease links come from ClinVar, Open Targets and UniProt, pooled from the latest public CATVariant analysis of each human protein. Evidence scores use the ACMG/AMP Bayesian points scale with computable criteria only (position among known disease variants, rarity in gnomAD, calibrated predictors, deep mutational scanning); there is no family or patient data, so they prioritise variants for expert review and never classify them.

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